Hydroxyurea with dose escalation for primary stroke risk reduction in children with sickle cell anaemia in Tanzania (SPHERE): an open-label, phase 2 trial. The Lancet Haematology. 2023; 10:e261-e271.
.2023; 142:2450.
. Inducible Knockout of Codanin-1: An Adult Mouse Model of Congenital Dyserythropoietic Anemia Type-I. Blood.2023; 7:100519.
. OC 38.4 Transient Antiphospholipid Antibodies, Antiphospholipid Syndrome and Clinical Outcomes in Patients <21 Years Old with Provoked Venous Thromboembolism: Analysis from the Kids-DOTT Multinational Trial. Research and Practice in Thrombosis and Haemostasis.2023; 142:1105.
. A Novel Beta Globin Frameshift Mutation Causing Autosomal Dominant Beta Thalassemia. Blood.Barriers to Genetic Testing in Vascular Malformations. JAMA network open. 2023; 6:e2314829.
.2023; 4:e067.
. RAND/UCLA Modified Delphi Panel on the Severity, Testing, and Medical Management of PIK3CA-Related Spectrum Disorders (PROS).2023; 7:101315.
. PB0727 The Role of Thrombin and Thrombin Signaling in Chronic LCMV Infection. Research and Practice in Thrombosis and Haemostasis.2023; 142:2459.
. Erythrocyte Disorders Mimicking Congenital Dyserythropoietic Anemia Based on Bone Marrow Pathology Exposed By Genetic Evaluation. Blood.Prevalence and Characteristics of Intracranial Aneurysms in Hereditary Hemorrhagic Telangiectasia. American Journal of Neuroradiology. 2023; 44:1367-1372.
.2023; 142:1242.
. Emicizumab Use in Infancy: A Survey of United States Pediatric Hemophilia Treatment Center Medical Directors. Blood.Vascular Anomalies Care in the United States: A Cross-Sectional National Survey. The Journal of Pediatrics. 2023; 261:113579.
.Return visit rates after an emergency department discharge for children with sickle cell pain episodes. Pediatric Blood and Cancer. 2023; 70:e30553.
.2023; 142:3874.
. Association between Acute Pain Scores in Children with Sickle Cell Disease and Emergency Department Disposition and Return Visit Rates. Blood.2023; 142:7198.
. Patterns of Nonadherence to Hydroxyurea in Pediatric Sickle Cell Disease. Blood.S. aureus drives itch and scratch-induced skin damage through a V8 protease-PAR1 axis. Cell. 2023; 186:5375-5393.e25.
.Hydroxyurea treatment for sickle cell anemia during pregnancy and lactation: Current evidence and knowledge gaps. Pharmacotherapy: The Journal of Human Pharmacology and Drug Therapy. 2023; 43:419-429.
.Genome-wide association study of early ischaemic stroke risk in Brazilian individuals with sickle cell disease implicates ADAMTS2 and CDK18 and uncovers novel loci. British Journal of Haematology. 2023; 201:343-352.
.2023; 142:1079.
. Congenital Dyserythropoietic Anemia Type II: An Update from the Congenital Dyseryhtropoietic Anemia Registry of North America (CDAR). Blood.Response to sirolimus in capillary lymphatic venous malformations and associated syndromes: Impact on symptomatology, quality of life, and radiographic response. Pediatric Blood and Cancer. 2023; 70:e30215.
.2023; 142:5055.
. Improving Transition of Emerging Adults with Sickle Cell Disease to Adult Care through a Multidisciplinary Process: The Development of a Transition Clinic to Support Transition Success. Blood.Hemostatic considerations for gender affirming care. Thrombosis Research. 2023; 230:126-132.
.Thrombin-mediated activation of PAR1 enhances doxorubicin-induced cardiac injury in mice. Blood Advances. 2023; 7:1945-1953.
.Mutations in the RACGAP1 gene cause autosomal recessive congenital dyserythropoietic anemia type III. Haematologica: the hematology journal. 2023; 108:581-587.
.Feasibility of Electronic Medication Monitoring Among Adolescents and Emerging Adults with Sickle Cell Disease. Patient Preference and Adherence. 2023; 17:3167-3171.
.Consensus definition of essential, optimal, and suggested components of a pediatric sickle cell disease center. Pediatric Blood and Cancer. 2023; 70:e29961.
.Navigating the marrow sea towards erythromyeloblastic islands under normal and inflammatory conditions. Current Opinion in Hematology. 2023; 30:80-85.
.2023; 142:920.
. Irf5 Expression in Macrophages Contributes to Iron Regulation within Erythromyeloblastic Islands. Blood.Illustrated State-of-the-Art Capsules of the ISTH 2023 Congress. Research and Practice in Thrombosis and Haemostasis. 2023; 7:100193.
.Comparing Characteristics and Treatment of Brain Vascular Malformations in Children and Adults with HHT. Journal of Clinical Medicine. 2023; 12.
.2023; 142:2593.
. Genetic Variants in Canonical Wnt Signaling Pathway Associated with Pediatric ITP. Blood.2023; 142:798.
. Grndad and Disease Modifying Therapy (DMT): Shifts in Dmt Are Seen at the Adolescent/Young Adult Transition in Sickle Cell Disease in a Multi-Site Prospective Registry. Blood.Improving bleeding disorder treatment log adherence: An application of the information-motivation-behavioral skills model. Haemophilia. 2023; 29:180-185.
.Consensus guidelines for diagnosis and management of anemia in epidermolysis bullosa. Orphanet Journal of Rare Diseases. 2023; 18:38.
.Human TLR8 induces inflammatory bone marrow erythromyeloblastic islands and anemia in SLE-prone mice. Life Science Alliance. 2023; 6.
.Kaposiform lymphangiomatosis: Diagnosis, pathogenesis, and treatment. Pediatric Blood and Cancer. 2023; 70:e30219.
.2023; 142:2530.
. A Novel, Rapid, and Accurate Quantitative Hydroxyurea Assay. Blood.Practice Variations in Managing Infantile Hemangiomas. Journal of Pediatric Hematology/Oncology. 2023; 45:452-460.
.Springer Nature; Springer Nature; 2023.
. Complex Thoracic Lymphatic Disorders of Adults. Orphan Lung Diseases. :2023; 7:101848.
. PB1495 Comfort and Experiences Providing Care to Transgender Youth Among Hematologists in the Midwestern United States. Research and Practice in Thrombosis and Haemostasis.2023; 142:3685.
. Attitudes of Hematologists in the Midwestern United States Toward Evaluating and Managing Thrombosis Risk in Transgender Youth Starting Gender Affirming Hormone Therapy. Blood.Zinc for infection prevention in children with sickle cell anemia: a randomized double-blind placebo-controlled trial. Blood Advances. 2023; 7:3023-3031.
.Executive summary of the 14th HHT international scientific conference. Angiogenesis. 2023; 26:27-37.
.Hydroxyurea treatment is associated with lower malaria incidence in children with sickle cell anemia in sub-Saharan Africa. Blood. 2023; 141:1402-1410.
.2023; 142:506.
. Once-Weekly Efanesoctocog Alfa Prophylaxis Provided High Sustained Factor VIII Activity Levels, Independent of Blood Group, in Children <12 Years of Age with Severe Hemophilia A. Blood.Defining global strategies to improve outcomes in sickle cell disease: a Lancet Haematology Commission. The Lancet Haematology. 2023; 10:e633-e686.
.Hydroxyurea: how much is enough?. Blood. 2023; 141:813-814.
.Safety and immunogenicity of V114, a 15-valent pneumococcal conjugate vaccine, in children with SCD: a V114-023 (PNEU-SICKLE) study. Blood Advances. 2023; 7:414-421.
.Implementation of CYP2D6-guided opioid therapy at Cincinnati Children's Hospital Medical Center. American Journal of Health-System Pharmacy. 2023; 80:852-859.
.Efficacy, safety, and pharmacokinetics of a new, ready-to-use, liquid hydroxyurea in children with sickle cell anemia. Blood Advances. 2023; 7:4319-4322.
.2023; 142:797.
. Hydroxyurea Improves Intelligence Quotient Scores in Children with Sickle Cell Anemia and Elevated Transcranial Doppler Velocity. Blood.Risk of Bacteremia in Febrile Children and Young Adults With Sickle Cell Disease in a Multicenter Emergency Department Cohort. JAMA network open. 2023; 6:e2318904.
.Hemolytic anemia and macrothrombocytopenia: A lipid problem?. American Journal of Hematology. 2023; 98:1335-1340.
.2023; 142:3832.
. Leveraging Transcriptomic Data to Study Erythromyeloblastic Island (EMBI) Macrophages: Using Spic-GFP As a Marker for Embi Macrophages. Blood.Crosstalk between terminal erythropoiesis and granulopoiesis within their common niche: the erythromyeloblastic island. Current Opinion in Hematology. 2023; 30:99-105.
.2023; 142:1145.
. Effects of L-Glutamine on Biomarkers of Response in Sickle Cell Disease: A Pharmacokinetics-Pharmacodynamics Analysis. Blood.Simultaneous adjunctive treatment of malaria and its coevolved genetic disorder sickle cell anemia. Blood Advances. 2023; 7:5970-5981.
.MEK inhibition reduced vascular tumor growth and coagulopathy in a mouse model with hyperactive GNAQ. Nature Communications. 2023; 14:1929.
.2023; 142:2270.
. Rapid Assessment of Hemoglobin-Oxygen Dissociation. Blood.2023; 7:101305.
. PB0708 The Tissue Factor/Thrombin Axis Limits Spontaneous Lymphatic Metastasis in Mice. Research and Practice in Thrombosis and Haemostasis.APC-PAR1-R46 signaling limits CXCL1 expression during poly IC-induced airway inflammation in mice. Journal of Thrombosis and Haemostasis. 2023; 21:3279-3282.
.2023; 142:1192.
. Immune Checkpoint Blockade Promotes Thrombosis Via T-Cell and Neutrophil Activation, and Tumor-Cell Associated Tissue Factor (TF) in a Murine Model of Colorectal Cancer. Blood.2023; 142:7199.
. SCD and COVID-19 Vaccines: What Do Pediatric Patients Want to Know?. Blood.Building the foundation for a community-generated national research blueprint for inherited bleeding disorders: research priorities for mucocutaneous bleeding disorders. Expert Review of Hematology. 2023; 16:39-54.
.Stroke Prevention with Hydroxyurea Enabled through Research and Education: A Phase 2 Primary Stroke Prevention Trial in Sub-Saharan Africa. Acta Haematologica. 2023; 146:95-105.
.Hydroxyurea pharmacokinetics and precision dosing in low-resource settings. Frontiers in Molecular Biosciences. 2023; 10:1130206.
. .Using the consolidated framework for implementation research to identify recruitment barriers and targeted strategies for a shared decision-making randomized clinical trial in pediatric sickle cell disease. Clinical Trials. 2023; 20:211-222.
.Iron status and burden of anemia in children with recessive dystrophic epidermolysis bullosa. Pediatric Dermatology. 2023; 40:288-293.
.The Role of Hereditary Hemorrhagic Telangiectasia in Neurologic Practice. Neurology. 2023; 100:1077-1078.
.Cost-Effectiveness of Hydroxyurea for Sickle Cell Anemia in a Low-Income African Setting: A Model-Based Evaluation of Two Dosing Regimens. Pharmacoeconomics Italian Research Articles. 2023; 41:1603-1615.
.Sirolimus in the Treatment of Microcystic Lymphatic Malformations: A Systematic Review. Lymphatic Research and Biology. 2023; 21:101-110.
.Codetection of Plasmodium falciparum in Children Hospitalized With Dengue Fever in the Dominican Republic. The Pediatric Infectious Disease Journal. 2023; 42:965-968.
.Barriers to medication adherence in children, adolescents, and young adults prescribed anticoagulation. Pediatric Blood and Cancer. 2023; 70:e30076.
.Lack of hydroxyurea-associated mutagenesis in pediatric sickle cell disease patients. Environmental and Molecular Mutagenesis. 2023; 64:167-175.
.An analysis of sex differences in pulmonary arteriovenous malformation presentation, complications and management in a large, multinational registry of patients with hereditary haemorrhagic telangiectasia. ERJ Open Research. 2023; 9.
.Targeting the contact system in a rabbit model of extracorporeal membrane oxygenation. Blood Advances. 2023; 7:1404-1417.
.Sustained and Boosted Antibody Responses in Breast Milk After Maternal SARS-CoV-2 Vaccination. Breastfeeding Medicine. 2023; 18:612-620.
.2023; 142:1275.
. Use and Outcomes of Secondary Anticoagulation in Patients <21 Years Old Following Completion of a Primary Course of Anticoagulation for Treatment of Acute Provoked VTE: Findings from the Multinational Kids-DOTT Trial. Blood.Pediatric myelofibrosis due to compound heterozygous MPIG6B mutations in a patient of European ancestry. Pediatric Blood and Cancer. 2023; 70:e30023.
.Genetic testing in the evaluation of individuals with clinical diagnosis of atypical Sturge-Weber syndrome. American Journal of Medical Genetics, Part A. 2023; 191:983-994.
.Evaluation of association of anti-PEG antibodies with anaphylaxis after mRNA COVID-19 vaccination. Vaccine. 2023; 41:4183-4189.
.