Cancer and Blood Diseases Institute

Publications

Abdullah, S; Sabulski, A; Hudda, Z; Ziady, A; Luebbering, N; Giordullo, L; Odegard, E; Blackard, JT; Kleiboeker, S; Altrich, M; Jodele, S; Seif, AE; Davies, SM; Laskin, BL. Susceptibility to BK polyomavirus-associated hemorrhagic cystitis in children undergoing allogeneic transplant. Haematologica: the hematology journal. 2025; 110:527-531.

Abdullah, S; Sabulski, DA; Hudda, DZ; Ziady, AG; Luebbering, N; Langenberg, L; Odegard, E; Blackard, JT; Kleiboeker, S; Jodele, S; Seif, AE; Davies, SM; Laskin, B. Bkpyv Replication Kinetics and Association with Hemorrhagic Cystitis in Pediatric HSCT Recipients. Transplantation and Cellular Therapy. 2025; 31:s515-s516.

Abts, MF; Silva Carmona, MD; Baker, KS; Ballard, S; Genatossio, A; Lane, A; Robinson, PD; Allen, JL; Koo, J; Davies, SM; Goldfarb, SB. Comparisons Between Multiple Breath Washout and Standard-of-Care Spirometry in Children Undergoing Allogenic Hematopoietic Stem Cell Transplant: A Transpire Study. American Journal of Respiratory and Critical Care Medicine. 2025; 211:a5125.

Agarwal, P; Sampson, A; Hueneman, K; Choi, K; Jakobsen, NA; Uible, E; Ishikawa, C; Yeung, J; Bolanos, L; Zhao, X; Galloway-Pena, J; Byrd, JC; Vyas, P; Starczynowski, DT. Microbial metabolite drives ageing-related clonal haematopoiesis via ALPK1. Nature. 2025; 642:201-211.

Aggarwal, RK; Sidoli, S; Wang, J; Sahu, S; Sanawar, R; Gupta, V; Aluri, S; Sukrithan, V; Vegivinti, CT R; Zavras, PD; LaFave, LM; Cheng, H; Verma, A; Zou, Y. Smoking-Associated Carcinogen-Induced Inflammation Promotes Lung Carcinogenesis via IRAK4 Activation. Clinical Cancer Research. 2025; 31:746-755.

Akyol, Ş; Yılmaz, E; Tokgöz, H; Karaman, K; Pekpak, E; Özcan, A; Şi̇mşek, A; Arslan, B; Ören, AC; Gökçeli̇, HS; Özdemi̇r, MA; Chiang, SC C; Bryceson, YT; Ünal, E. Clinical spectrum of primary hemophagocytic lymphohistiocytosis: experience of reference centers in Central and Southeast Anatolia. Annals of Hematology. 2025; 104:123-130.

Alexander, JL; Saldana, BJ D; Brazauskas, R; Dammalapati, SG; Griffith, LM; Shah, AJ; Shimano, KA; Ochs, HD; Bleesing, JJ; Ebens, CL; Petrovic, A; Pai, S; Burroughs, LM; Chan, A. Hematopoietic Cell Transplantation for Wiskott-Aldrich Syndrome - Impact of Age, Donor, and Infection: A Pidtc Report. Transplantation and Cellular Therapy. 2025; 31:s39-s41.

Alharbi, S; Merkle, S; Hammill, AM; Waters, AM; Le Cras, TD. RAS Pathway Mutations and Therapeutics in Vascular Anomalies. Pediatric Blood and Cancer. 2025; 72:e31605.

Almohtasib, J; Indelicato, DJ; Paulino, AC; Mihalcik, S; Lee, J; Ermoian, R; Chang, JH C; Kwok, Y; Perentesis, J; Perkins, SM; Hill-Kayser, C; Zeina, W; Laack, NN; Yock, TI; Gargollo, PC. Assessing Acute and Long-Term Toxicities of Proton Radiation Therapy in Pediatric Pelvic Tumors: Findings From the Pediatric Proton Consortium Registry. Pediatric Blood and Cancer. 2025; e31811.

Ambrose, EE; Sabuni, PA; Jason, DP; Ware, RE; Makubi, AN; Smart, LR. Hydroxyurea to decrease stroke risk in children with sickle cell anemia: a systematic review and meta-analysis. 2025; 1:100001.

Armstrong, AE; Daw, NC; Renfro, LA; Geller, JI; Kalapurakal, JA; Khanna, G; Paulino, AC; Perlman, EJ; Ehrlich, PF; Gow, KW; Warwick, AB; Grundy, PE; Fernandez, CV; Mullen, EA; Dome, JS. Treatment of focal anaplastic Wilms tumor: A report from the Children's Oncology Group AREN0321 and AREN03B2 studies. Cancer. 2025; 131:e35713.

Ashraf, A; Davies, SM; Jodele, S; Sabulski, DA. A 10-Year History of Graft Failure in Pediatric Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:s148-s149.

Ashraf, A; Lake, KE; Myers, KC; Towe, C; Cooper, R; Edwards, MS L; Hils, B; Davies, SM; Koo, DJ. Frequent Pulmonary Complications after Allogeneic Hematopoietic Stem Cell Transplant: A Brief Transpire Report. Transplantation and Cellular Therapy. 2025; 31:s149-s150.

Ashraf, A; Murphey, C; Sper, C; Webster, A; Lane, A; Mesa, S; Garcia, F; Perez, MR; Chamblin, C; Davies, SM; Khandelwal, P. Male Gender and Underlying Diagnosis Predisposes to Increased HLA Antibody Burden in Children before Allogeneic Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:s147.

Babic, I; Bryan, N; Cunningham, C; Sampson, A; Starczynowski, D; Nurmemmedov, E. Abstract 5480: Live cell real-time quantification of drug-target engagement for rapid drug discovery. Cancer Research. 2025; 85:5480.

Bacha, J; Brown, D; Geller, J; Oesterheld, J; Thompson, P; Kim, A; McManus, M; Kanekal, S; Leggas, M; Lopez, L; Sankar, N; Yam, N; Wagner, L. Abstract LB266: A multicenter phase 1-2a clinical study of Orotecan® (oral irinotecan HCl, VAL-413) in patients with recurrent pediatric solid tumors. Cancer Research. 2025; 85:lb266.

Bahakel, H; Spieker, AJ; Hayek, H; Schuster, JE; Hamdan, L; Dulek, DE; Kitko, CL; Stopczynski, T; Batarseh, E; Haddadin, Z; Englund, JA; Munoz, FM; Danziger-Isakov, L; Halasa, N. Immunogenicity and Reactogenicity of High- or Standard-Dose Influenza Vaccine in a Second Consecutive Influenza Season. The Journal of Infectious Diseases. 2025; 231:e123-e131.

Bauchat, A; Peterson, A; Ahn, KW; Mehta, PA; Phillips, CL; Schultz, KR; Sharma, A; Broglie, L; Qayed, M. Impact of Graft Versus Host Disease Following Allogeneic Hematopoietic Cell Transplantation on Leukemia Free Survival in Hematologic Malignancies: A CIBMTR Analysis. Transplantation and Cellular Therapy. 2025; 31:s60-s61.

Bedard, MC; Rivera-Cruz, CM; Chihanga, T; VonHandorf, A; Tang, AL; Zender, C; Weirauch, MT; Ferris, R; Wise-Draper, TM; Adam, M; Wells, SI. A Single-Cell Transcriptome Atlas of Epithelial Subpopulations in HPV-Positive and HPV-Negative Head and Neck Cancers. Viruses-Basel. 2025; 17:461.

Bender, J; Davies, SM; Myers, KC; Benoit, SW. Beyond Survival: Assessing Renal and Cardiovascular Health in Fanconi Anemia Adolescents and Young Adults Post-Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:s375-s376.

Bhatt, N; Hellewell, EM; Ng, K; Gooley, TA; Taylor, AO; Hong, S; Sung, A; Ahmed, N; Morey, C; Fitzmaurice, S; Yingling, S; Edgar, C; Browning, A; Lee, CJ. Real-World Assessment of Patient Adherence to the Late Effects Screening Recommendations Among Hematopoietic Cell Transplantation Survivors. Transplantation and Cellular Therapy. 2025; 31:s364-s365.

Bhatt, NS; Lehmann, L; Dandoy, CE; Auletta, JJ; Badia, P; Ballard, SA; Blacken, R; Daraiseh, NM; Desmond, C; Dunseath, C; Tarquini, S; Phelan, R; Pai, A; Rotz, S. Multicenter Study on Caregiver Experiences in Pediatric Hematopoietic Stem Cell Transplantation Part I: Integrative Analysis of Mental Health, Psychosocial Stressors, and Support Mechanisms. Transplantation and Cellular Therapy. 2025; 31:456.e1-456.e16.

Bleesing, J. The Fas-mediated apoptosis assay: From concept to clinical application. Journal of Immunological Methods. 2025; 537:113812.

Blumenstock, JA; Boge, C; Shuster, S; Li, Y; Seif, AE; Green, MD; Michaels, MG; Alexander, JL; Ardura, MI; Auletta, J; Kajon, AE; Grimley, M; Danziger-Isakov, LA; Fisher, BT. 633. Incidence and Outcomes of Pediatric Allogeneic Hematopoietic Cell Transplant (allo-HCT) Recipients Under Surveillance and Not Under Surveillance for Human Adenovirus (HAdV) in the Post-HCT Period. Open Forum Infectious Diseases. 2025; 12:ofae631.198.

Boldt, A; Bender, J; Jodele, S; Davies, SM; Benoit, SW. Differential Filtration of Macromolecules: A Novel Indicator of Mortality Risk in Pediatric HSCT Patients. Transplantation and Cellular Therapy. 2025; 31:s145-s146.

Borate, U; Pugh, K; Waller, A; Welkie, RL; Huang, Y; Bewersdorf, JP; Stahl, M; DeZern, AE; Platzbecker, U; Sekeres, MA; Bennett, JM; List, AF; Brunner, AM; Zeidan, AM. Reducing clinical trial eligibility barriers for patients with MDS: an icMDS position statement. Blood. 2025; 145:1369-1381.

Bosticardo, M; Dobbs, K; Delmonte, OM; Martins, AJ; Pala, F; Kawai, T; Kenney, H; Magro, G; Rosen, LB; Yamazaki, Y; Preece, K; Prockop, S; Sakovich, IS; Starkova, EE. Multiomics dissection of human RAG deficiency reveals distinctive patterns of immune dysregulation but a common inflammatory signature. Science immunology. 2025; 10:eadq1697.

Boucher, AA; Dayton, VJ; Pratt, AR; Nassar, NN; Elgammal, Y; Kalfa, TA. Three-generation female cohort with macrocytic anemia and iron overload. American Journal of Hematology. 2025; 100:133-138.

Brown, A; Pommert, L. GATA Lot to Learn: Decoding the Drivers of Down Syndrome-Associated Acute Leukemias. 2025; 22.

Brown, M; Grassia, K; Miller, J; Hall, E; Dewan, M; Dandoy, C; Zhang, B; Finnsdottir Wagner, A. 1187: ECMO IN PEDIATRIC ONCOLOGIC AND HEMATOPOIETIC STEM CELL TRANSPLANT PATIENTS: A COMPARATIVE ANALYSIS. Critical Care Medicine. 2025; 53.

Cai, M; Adam, M; Guo, F; Zheng, Y. Abstract 1596: Tumor-derived RAC1A159V gain-of-function mutation promotes an immunosuppressive tumor microenvironment and represses response to immune checkpoint inhibitors. Cancer Research. 2025; 85:1596.

Canaud, G; López-Gutiérrez, JC; Hammill, A; Weibel, L; Niglis, S; Paul, M; Papadimitriou, A; Wroclawska, M; Caro, N; Adams, D. 118: Randomized, Double-Blind, Phase 2 Study of Alpelisib in Pediatric and Adult Patients With PIK3CA-Related Overgrowth Spectrum (PROS). Journal of Investigative Dermatology. 2025; 145:e29.

Cantrell, R; Alex Feldman, H; Rosenfeldt, L; Ali, A; Gourley, B; Sprague, C; Leino, D; Crosby, J; Revenko, A; Monia, B; Waggoner, SN; Palumbo, JS. Prothrombin prevents fatal T cell-dependent anemia during chronic virus infection of mice. JCI insight. 2025; 10:e181063.

Chan, AK; Susen, S; Khoo, L; von Drygalski, A; Oldenburg, J; Shen, M; Peyvandi, F; Tarango, C; Chowdary, P; Mamikonian, L; Palmborg, H; Dumont, J; Santagostino, E; Hermans, C. Perioperative Management with Efanesoctocog Alfa in Adults, Adolescents, and Children with Severe Hemophilia A in the Phase 3 XTEND Clinical Program. Hamostaseologie. 2025; 45:s57-s58.

Chandrakasan, S; Allen, CE; Bhatla, D; Carter, J; Chien, M; Cooper, R; Draper, L; Eckstein, OS; Hanna, R; Hays, JA; Riskalla, M; Hobday, P; Baker, A; Ward, B. Emapalumab Treatment in Patients With Rheumatologic Disease-Associated Hemophagocytic Lymphohistiocytosis in the United States: A Retrospective Medical Chart Review Study. Arthritis and Rheumatology. 2025; 77:226-238.

Chen, F; Liu, X; Zhong, X; Chen, X; Nicholson, E; Liu, K; Chen, H; Lin, Y; Shu, Y; Zhou, W; Schuurmans, CJ; Lu, QR. Neurons derived from NeuroD1-expressing astrocytes transition through transit-amplifying intermediates but lack functional maturity. Science Advances. 2025; 11:eadw9296.

Chen, Z; Zeng, C; Yang, L; Che, Y; Chen, M; Sau, L; Wang, B; Zhou, K; Chen, Y; Qing, Y; Weng, H; Xiao, G; Deng, X; Chen, J. YTHDF2 promotes ATP synthesis and immune evasion in B cell malignancies. Cell. 2025; 188:331-351.e30.

Chi, M; Malik, P. An engineered β-globin homology donor reveals insights into β-globin expression and betters HDR. Molecular Therapy. 2025; 33:1308-1309.

Chiang, S; Akeno, N; Owsley, E; Verbsky, J; Ibrahimova, A; Bleesing, J; Marsh, R. Clinical and Analytical Validation of a NOD2 Functional Test for XIAP/XLP2 Diagnosis. 2025; 1.

Chiang, S; Yang, L; Akeno, N; Owsley, E; de Jesus, A; Goldbach-Mansky, R; Marsh, R; Bleesing, J. Validation of an Interferon Type I Score Test on the Nanostring nCounter Platform. 2025; 1.

Chiang, SC C; Yang, L; Owsley, E; Husami, A; Akeno, N; Cobb, C; Hartog, NL; Elizalde, A; Seroogy, CM; Blanchard-Rohner, G; Marsh, R; Bleesing, J; Jordan, MB; Marwaha, AK. Lipopolysaccharide-responsive and beige-like anchor protein (LRBA) functional deficiency caused by biallelic LRBA missense variants characterized by Evans syndrome or colitis. Journal of Allergy and Clinical Immunology. 2025; 156:270-278.

Childress, A; Koch, A; Vallee, E; Steller, A; Raskin, S. The Current Landscape of Molecular Pathology for the Diagnosis and Treatment of Atypical Teratoid Rhabdoid Tumor. Journal of Molecular Pathology. 2025; 6:13.

Choi, J; Koo, J. Protein-Protein Interactions of Odorant and G Protein-Coupled Receptors: A BRET Analysis Approach. Methods in molecular biology (Clifton, N.J.). 2025; 2915:161-168.

Choi, J; Koo, J. Yellow Fluorescent Protein Quenching Assay for Analyzing Odorant Receptor Activity. Methods in molecular biology (Clifton, N.J.). 2025; 2915:169-177.

Chowdhury, I; Jakobsen, ER; Krupski, M. A strongly degenerate fully nonlinear mean field game with nonlocal diffusion. Journal of Differential Equations. 2025; 440:113436.

Clough, CA; Cunningham, C; Philbrook, SY; Hueneman, KM; Sampson, AM; Choi, K; Greis, KD; Starczynowski, D. Characterization of E1 enzyme dependencies in mutant-UBA1 human cells reveals UBA6 as a novel therapeutic target in VEXAS syndrome. Leukemia. 2025; 39:1997-2009.

COHEN, RM; CRAIG, J; OMOLOLU, SO; TOZZO, V; SMITH, EP; ARBABI, S; GENCO, M; ABPLANALP, W; THIBAULT, D; QUINN, CT; LINDSELL, CJ; BERGENSTAL, RM; FRANCO, RS; HIGGINS, J. 166-OR: Mean RBC Age (MRBC) Variation Accounts for the Predominance of Mismatch (MM) between Measured HbA1c (mA1c) and CGM-Derived Estimated HbA1c (eA1c). Diabetes. 2025; 74.

Coleman, KD; McKinley, K; Ellison, AM; Alpern, ER; Hariharan, S; Topoz, I; Wurtz, M; Nielsen, B; Cook, LJ; Morris, CR; King, AA; Baumann, A; Frankenberger, W; Brousseau, DC. Associations Between Pain Scores and Opioid Doses With Emergency Department Disposition and Return Visit Rates in Children With Sickle Cell Disease. Pediatric Blood and Cancer. 2025; 72:e31750.

Cook, E; Haacker, L; Chandra, S; Jordan, MB; Verkamp, B; McCarthy, L; Rotz, SJ; Hammoud, MS; Pariury, H; McKeone, D; Kumar, A. EBV-Associated T/NK-LPD Manifesting As HLH Cured By Nivolumab and Emapalumab, Avoiding the Need for Allogeneic HCT. Transplantation and Cellular Therapy. 2025; 31:s43.

Cook, E; Langenberg, L; Luebbering, N; Ibrahimova, A; Myers, KC; Sabulski, A; Dandoy, C; Lake, K; Ziady, A; Lane, A; Webster, A; Abdullah, S; Jodele, S; Davies, SM. Oxidative Stress Early After Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:135.e1-135.e10.

Cook, E; Schulert, G; Grom, A; Towe, C; Burg, G; Marsh, R; Chandra, S. Experience with T Cell–Depleted Allogeneic HSCT for Refractory sJIA Associated with Lung Disease. 2025; 1.

Costa, E; Ware, RE; Tshilolo, L; Makani, J; Leufkens, HG M; Luzzatto, L. Globalization in clinical drug development for sickle cell disease. American Journal of Hematology. 2025; 100:4-9.

D’Alessandro, PR; Homanick, CE; Cooper, BD; Ferguson, K; Rutan, H; Pressey, JG. "From Drowning to Treading Water ": Adolescents and Young Adults Living with Incurable and Indolent Metastatic Soft Tissue Sarcoma for More than Two Years. Cancers. 2025; 17:442.

Dandoy, CE; Auletta, JJ; Badia, P; Bidgoli, A; Daraiseh, NM; DeSalvo, AM; Diaz, J; Davies, SM; Demmel, K; Cook, E; Salem, BM; Snyder, A; Juckett, M; Hartley, D. Engraft: A Collaborative Learning Health Network for Enhanced Transplant and Cellular Therapy Outcomes. Transplantation and Cellular Therapy. 2025; 31:123-134.

Davies, SM; Grimley, MS; Shrestha, A; Shova, A; Asnani, M; Kent, M; Sayani, F; Quinn, CT; Niss, O; Lutzko, CM; Witting, S; Latham, T; Bushman, FD; Malik, P. Gene Therapy with Reduced-Intensity Conditioning for Sickle Cell Disease. Transplantation and Cellular Therapy. 2025; 31:s2-s3.

Dávila Saldaña, BJ; Schultz, KR; Ramgopal, A; Boiko, JR; Beebe, K; Carpenter, PA; Chan, SS; Paczesny, S; Aguayo-Hiraldo, P; Cuvelier, GD E; Rotz, SJ; Duncan, CN; Williams, KM. Pediatric Transplant and Cellular Therapy Consortium RESILIENT Conference on Pediatric Chronic Graft-versus-Host Disease Survivorship after Hematopoietic Cell Transplantation: Part II. Organ Dysfunction and Immune Reconstitution Considerations for Children with Chronic Graft-versus-Host Disease after Hematopoietic Cell Transplantation. Transplantation and Cellular Therapy. 2025; 31:347.e1-347.e17.

Davis, K; Molloy, E; Marks, K; Breese, E; Michael Taylor, J; Broomall, E; Stalets, E. 667: SEVERE METHOTREXATE-INDUCED NEUROTOXICITY IN A HISPANIC ADOLESCENT GIRL WITH B-ALL. Critical Care Medicine. 2025; 53.

Dei-Adomakoh, YA; Segbefia, CI; Latham, TS; Lane, AC; Dzefi-Tettey, K; Amissah-Arthur, K; Corquaye, O; Korang, L; Mensah, E; Ekpale, P; Seedah, D; Stuber, SE; Smart, LR; Ware, RE. Hydroxyurea for Children and Adults with Hemoglobin SC Disease. 2025; 4:EVIDoa2400402.

Dela Cruz, FS; Fox, E; DuBois, SG; Friedman, GK; Croop, JM; Kim, AR; Morgenstern, DA; Balis, FM; Macy, ME; Pressey, JG; He, CS; Aluri, J; Okpara, CE; Glade Bender, JL. A Phase 1/2 Study of Lenvatinib in Combination With Everolimus in Recurrent and Refractory Pediatric and Young Adult Solid Tumors. Pediatric Blood and Cancer. 2025; 72:e31692.

Djassemi, N; Kinoshita, H; Maghzian, N; Datar, A; Joy, E; McCann, C; Shibli, A; Saldana, BD; Hoq, F; Hanley, PJ; Pulsipher, MA; Bollard, CM; Keller, MD. Outcome Analysis Post Virus-Specific T Cell Therapy for the Treatment of Adenoviremia in Immunocompromised Pediatric Patients. Transplantation and Cellular Therapy. 2025; 31:s221-s222.

Dombi, E; Gross, AM; Widemann, BC; Weiss, BD; Plotkin, SR; Ahlawat, S. Challenges in Assessing Response in Clinical Trials for Neurofibromatosis Type 1 Plexiform Neurofibromas. Journal of Clinical Oncology. 2025; 43:1843-1844.

Drozdov, D; Luo, X; Marsh, RA; Abraham, RS; Ebens, CL. Relevance of Recent Thymic Emigrants Following Allogeneic Hematopoietic Cell Transplantation for Pediatric Patients with Inborn Errors of Immunity. Transplantation and Cellular Therapy. 2025; 31:265.e1-265.e12.

Durkee-Shock, J; Cohen, A; Maghzian, N; Pezzella, G; Jensen-Wachspress, M; Hostal, A; Barton, K; Gangler, K; Dávila Saldaña, BJ; Chaimongkol, N; Gonzalez, C; Notarangelo, LD; Green, KY; Keller, MD. Reconstitution of Norovirus-Specific T-Cell Responses Following Hematopoietic Stem Cell Transplantation in Patients With Inborn Errors of Immunity and Chronic Norovirus Infection. The Journal of Infectious Diseases. 2025; 231:773-783.

Eigenbrood, J; Wong, N; Mallory, P; Pereira, JS; Williams, D; Morris, DW; Beck, JA; Cronk, JC; Sayers, CM; Mendez, M; LeBlanc, AK; Cotter, J; Kaplan, RN; McEachron, TA. Spatial Profiling Identifies Regionally Distinct Microenvironments and Targetable Immunosuppressive Mechanisms in Pediatric Osteosarcoma Pulmonary Metastases. Cancer Research. 2025; 85:2320-2337.

Engel, ER; Luchtman-Jones, L. Comment on: "Comment on: Bivalirudin During Thrombolysis With Catheter-Directed tPA in a Heparin-Refractory Patient: A Case Report ": The Promise of Dilute Thrombin Time and Drug-Calibrated Assays for Improved Bivalirudin Monitoring. Pediatric Blood and Cancer. 2025; 72:e31418.

Fathi Kazerooni, A; Khalili, N; Liu, X; Haldar, D; Jiang, Z; Zapaishchykova, A; Pavaine, J; Shah, LM; Jones, BV; Sheth, N; Resnick, A; Bakas, S; Vossough, A; Linguraru, MG. BraTS-PEDs: Results of the Multi-Consortium International Pediatric Brain Tumor Segmentation Challenge 2023. 2025; 3:72-87.

Fernandez, K; Hoetink, A; Konrad-Martin, D; Berndtson, D; Clark, K; Dreisbach, L; Geller, JI; Goffi-Gomez, MV; Grosnik, A; Jamis, C; Sanchez, VA; Van Den Heuvel-Eibrink, MM; Brewer, CC; Poling, GL. Roadmap to a Global Template for Implementation of Ototoxicity Management for Cancer Treatment. Ear and Hearing. 2025; 46:286-297.

Fidler, AL; O'Connor, G; Beebe, DW; Wang, YZ M; Crosby, LE; Dandoy, CE. How to Improve the Sleep of Hospitalized Pediatric Patients: Family and Staff Focus Groups. Transplantation and Cellular Therapy. 2025; 31:586.e1-586.e11.

Fisher, AA; Gonzalez, LS; Cappel, ZR; Grover, KE; Waclaw, RR; Robinson, JE. Dopaminergic encoding of future defensive actions in the mouse nucleus accumbens. Editor, Bahar I. PNAS Nexus. 2025; 4:pgaf128.

Fleifil, Y; Gulati, R; Jennings, K; Miethke, A; Bondoc, A; Tiao, G; Geller, JI; Karns, R; Timchenko, L; Timchenko, N. DNAJB1-PKAc Kinase Is Expressed in Young Patients with Pediatric Liver Cancers and Enhances Carcinogenic Pathways. Cancers. 2025; 17:83.

Fragneau, R; Fraitag, S; Kemps, PG; Hélias-Rodzewicz, Z; Roy, S; Bonsang, B; Bartlett, AL; Dhar, S; Jankofsky, M; Zlocha, J; Donadieu, J; Borkhardt, A; Picarsic, JL; Emile, JF. NTRK1-rearranged histiocytosis: clinicopathologic and molecular features. Blood Advances. 2025; 9:3617-3628.

Freyer, DR; Ohlsen, TJ D; Don, D; Orgel, E; Hayashi, RJ; Lieu, JE; Foster, JH; Sitton, MS; Geller, JI; Choo, DI; Grunstein, E; O'Neill, AF; Rahbar, R; Anderson, JJ. Feasibility and Safety of Intratympanic Administration of Sustained-Exposure Dexamethasone Thermosensitive Gel (OTO-104) for Prevention of Cisplatin-Induced Hearing Loss in Children: A Multisite Phase 2 Randomized Clinical Trial. Pediatric Blood and Cancer. 2025; 72:e31680.

Galletta, TJ; Benoit, SW; Markham, J; Pillay-Smiley, N; Queen, K; Graham, RT. Elevated Bromide Levels Due to Tazemetostat Therapy Treated With Salt and Water Supplementation in Two Children With Atypical Teratoid Rhabdoid Tumor. Pediatric Blood and Cancer. 2025; 72:e31803.

Garrett, MC; Carnwath, T; Albano, R; Zhuang, Y; Behrmann, CA; Pemberton, M; Barakat, F; Lober, R; Hoeprich, M; Paravati, A; Perentesis, J; Nasser, R; Medvedovic, M; Plas, DR. CPI203, a BET inhibitor, down-regulates a consistent set of DNA synthesis genes across a wide array of glioblastoma lines. Editor, Li M. PloS one. 2025; 20:e0306846.

Geller, JI; Renfro, LA; Grundy, PE; Perlman, EJ; Kalapurakal, JA; Ehrlich, PF; Biegel, J; Huff, V; Warwick, AB; Paulino, A; Ward, DA; Anderson, JR; Fernandez, CV; Dome, JS. Rhabdoid Tumor of the Kidney and Soft Tissues: Results from National Wilms Tumor Study-5 and Children's Oncology Group Study AREN0321. Pediatric Blood and Cancer. 2025; 72:e31490.

Ghosh, A; Li, H; Towbin, A; Turpin, B; Trout, A. T2-weighted MRI radiomics for the prediction of pediatric and young adult rhabdomyosarcoma alveolar subtype and distant metastasis: a pilot study. Pediatric Radiology: roentgenology, nuclear medicine, ultrasonics, CT, MRI. 2025; 55:1149-1161.

Gilene, S; Haacker, L; Rutan, H; Pressey, JG. The Threat of Medical Misinformation: A Case of Ivermectin Toxicity in a Pediatric Oncology Patient. Pediatric Blood and Cancer. 2025; 72:e31876.

Gilene, S; Knapke, S; Leino, D; Roy, S; Raskin, S. A novel POT1-TPD presentation: A germline pathogenic POT1 variant discovered in a patient with newly diagnosed posterior fossa ependymoma. Cancer genetics. 2025; 292-293:38-43.

Ginocchio, MP; Gutarra, ME; Ramos, KN; Shah, R; Pandey, M; Ghalehsari, N; Davies, SM; Auletta, DJ J; Hall, AG; Arteaga, AG. Understanding Diversity: An ASTCT-NMDP Access Initiative Survey of the Hematopoietic Cell Transplant and Cellular Therapy Nonphysician Workforce. Transplantation and Cellular Therapy. 2025; 31:s343-s344.

Ginocchio, MP; Ramos, KN; Gutarra, ME; Ghalehsari, N; Pandey, M; Shah, R; Davies, SM; Auletta, DJ J; Arteaga, AG; Hall, AG. Physician Workforce Diversity in the Hematopoietic Cell Transplant and Cellular Therapy Ecosystem: An ASTCT-NMDP Access Initiative Survey. Transplantation and Cellular Therapy. 2025; 31:s361.

Goda, C; Kulkarni, R; Bustos, Y; Li, W; Rudich, A; Balcioglu, O; Chidester, S; Urs, AP; Karunasiri, M; Al-Marrawi, Y; Viny, AD; Miles, LA; Miller, KE; Dorrance, AM. Cellular taxonomy of the preleukemic bone marrow niche of acute myeloid leukemia. Leukemia. 2025; 39:51-63.

Goldenberg, NA; Schulman, S; Kittelson, JM; Abshire, TC; Casella, JF; Dale, R; Halperin, JL; Hanson, J; Kessler, CM; Manco-Johnson, MJ; McDevitt, L; Sidonio, RF; Spyropoulos, AC; Steg, PG; Bonaca, MP. Duration of anticoagulation for venous thromboembolism in pediatric patients: Evaluation of the Duration of Therapy for Thrombosis in Children (Kids-DOTT) trial outcomes at 2 years. Journal of Thrombosis and Haemostasis. 2025; 23:651-656.

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