Bone Marrow Transplantation and Immune Deficiency

Publications

Abdullah, S; Sabulski, A; Hudda, Z; Ziady, A; Luebbering, N; Giordullo, L; Odegard, E; Blackard, JT; Kleiboeker, S; Altrich, M; Jodele, S; Seif, AE; Davies, SM; Laskin, BL. Susceptibility to BK polyomavirus-associated hemorrhagic cystitis in children undergoing allogeneic transplant. Haematologica: the hematology journal. 2025; 110:527-531.

Abdullah, S; Sabulski, DA; Hudda, DZ; Ziady, AG; Luebbering, N; Langenberg, L; Odegard, E; Blackard, JT; Kleiboeker, S; Jodele, S; Seif, AE; Davies, SM; Laskin, B. Bkpyv Replication Kinetics and Association with Hemorrhagic Cystitis in Pediatric HSCT Recipients. Transplantation and Cellular Therapy. 2025; 31:s515-s516.

Abts, MF; Silva Carmona, MD; Baker, KS; Ballard, S; Genatossio, A; Lane, A; Robinson, PD; Allen, JL; Koo, J; Davies, SM; Goldfarb, SB. Comparisons Between Multiple Breath Washout and Standard-of-Care Spirometry in Children Undergoing Allogenic Hematopoietic Stem Cell Transplant: A Transpire Study. American Journal of Respiratory and Critical Care Medicine. 2025; 211:a5125.

Akyol, Ş; Yılmaz, E; Tokgöz, H; Karaman, K; Pekpak, E; Özcan, A; Şi̇mşek, A; Arslan, B; Ören, AC; Gökçeli̇, HS; Özdemi̇r, MA; Chiang, SC C; Bryceson, YT; Ünal, E. Clinical spectrum of primary hemophagocytic lymphohistiocytosis: experience of reference centers in Central and Southeast Anatolia. Annals of Hematology. 2025; 104:123-130.

Alexander, JL; Saldana, BJ D; Brazauskas, R; Dammalapati, SG; Griffith, LM; Shah, AJ; Shimano, KA; Ochs, HD; Bleesing, JJ; Ebens, CL; Petrovic, A; Pai, S; Burroughs, LM; Chan, A. Hematopoietic Cell Transplantation for Wiskott-Aldrich Syndrome - Impact of Age, Donor, and Infection: A Pidtc Report. Transplantation and Cellular Therapy. 2025; 31:s39-s41.

Ashraf, A; Davies, SM; Jodele, S; Sabulski, DA. A 10-Year History of Graft Failure in Pediatric Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:s148-s149.

Ashraf, A; Lake, KE; Myers, KC; Towe, C; Cooper, R; Edwards, MS L; Hils, B; Davies, SM; Koo, DJ. Frequent Pulmonary Complications after Allogeneic Hematopoietic Stem Cell Transplant: A Brief Transpire Report. Transplantation and Cellular Therapy. 2025; 31:s149-s150.

Ashraf, A; Murphey, C; Sper, C; Webster, A; Lane, A; Mesa, S; Garcia, F; Perez, MR; Chamblin, C; Davies, SM; Khandelwal, P. Male Gender and Underlying Diagnosis Predisposes to Increased HLA Antibody Burden in Children before Allogeneic Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:s147.

Bahakel, H; Spieker, AJ; Hayek, H; Schuster, JE; Hamdan, L; Dulek, DE; Kitko, CL; Stopczynski, T; Batarseh, E; Haddadin, Z; Englund, JA; Munoz, FM; Danziger-Isakov, L; Halasa, N. Immunogenicity and Reactogenicity of High- or Standard-Dose Influenza Vaccine in a Second Consecutive Influenza Season. The Journal of Infectious Diseases. 2025; 231:e123-e131.

Bauchat, A; Peterson, A; Ahn, KW; Mehta, PA; Phillips, CL; Schultz, KR; Sharma, A; Broglie, L; Qayed, M. Impact of Graft Versus Host Disease Following Allogeneic Hematopoietic Cell Transplantation on Leukemia Free Survival in Hematologic Malignancies: A CIBMTR Analysis. Transplantation and Cellular Therapy. 2025; 31:s60-s61.

Bender, J; Davies, SM; Myers, KC; Benoit, SW. Beyond Survival: Assessing Renal and Cardiovascular Health in Fanconi Anemia Adolescents and Young Adults Post-Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:s375-s376.

Bhatt, N; Hellewell, EM; Ng, K; Gooley, TA; Taylor, AO; Hong, S; Sung, A; Ahmed, N; Morey, C; Fitzmaurice, S; Yingling, S; Edgar, C; Browning, A; Lee, CJ. Real-World Assessment of Patient Adherence to the Late Effects Screening Recommendations Among Hematopoietic Cell Transplantation Survivors. Transplantation and Cellular Therapy. 2025; 31:s364-s365.

Bhatt, NS; Lehmann, L; Dandoy, CE; Auletta, JJ; Badia, P; Ballard, SA; Blacken, R; Daraiseh, NM; Desmond, C; Dunseath, C; Tarquini, S; Phelan, R; Pai, A; Rotz, S. Multicenter Study on Caregiver Experiences in Pediatric Hematopoietic Stem Cell Transplantation Part I: Integrative Analysis of Mental Health, Psychosocial Stressors, and Support Mechanisms. Transplantation and Cellular Therapy. 2025; 31:456.e1-456.e16.

Bleesing, J. The Fas-mediated apoptosis assay: From concept to clinical application. Journal of Immunological Methods. 2025; 537:113812.

Blumenstock, JA; Boge, C; Shuster, S; Li, Y; Seif, AE; Green, MD; Michaels, MG; Alexander, JL; Ardura, MI; Auletta, J; Kajon, AE; Grimley, M; Danziger-Isakov, LA; Fisher, BT. 633. Incidence and Outcomes of Pediatric Allogeneic Hematopoietic Cell Transplant (allo-HCT) Recipients Under Surveillance and Not Under Surveillance for Human Adenovirus (HAdV) in the Post-HCT Period. Open Forum Infectious Diseases. 2025; 12:ofae631.198.

Boldt, A; Bender, J; Jodele, S; Davies, SM; Benoit, SW. Differential Filtration of Macromolecules: A Novel Indicator of Mortality Risk in Pediatric HSCT Patients. Transplantation and Cellular Therapy. 2025; 31:s145-s146.

Bosticardo, M; Dobbs, K; Delmonte, OM; Martins, AJ; Pala, F; Kawai, T; Kenney, H; Magro, G; Rosen, LB; Yamazaki, Y; Preece, K; Prockop, S; Sakovich, IS; Starkova, EE. Multiomics dissection of human RAG deficiency reveals distinctive patterns of immune dysregulation but a common inflammatory signature. Science immunology. 2025; 10:eadq1697.

Brown, M; Grassia, K; Miller, J; Hall, E; Dewan, M; Dandoy, C; Zhang, B; Finnsdottir Wagner, A. 1187: ECMO IN PEDIATRIC ONCOLOGIC AND HEMATOPOIETIC STEM CELL TRANSPLANT PATIENTS: A COMPARATIVE ANALYSIS. Critical Care Medicine. 2025; 53.

Chandrakasan, S; Allen, CE; Bhatla, D; Carter, J; Chien, M; Cooper, R; Draper, L; Eckstein, OS; Hanna, R; Hays, JA; Riskalla, M; Hobday, P; Baker, A; Ward, B. Emapalumab Treatment in Patients With Rheumatologic Disease-Associated Hemophagocytic Lymphohistiocytosis in the United States: A Retrospective Medical Chart Review Study. Arthritis and Rheumatology. 2025; 77:226-238.

Chiang, S; Akeno, N; Owsley, E; Verbsky, J; Ibrahimova, A; Bleesing, J; Marsh, R. Clinical and Analytical Validation of a NOD2 Functional Test for XIAP/XLP2 Diagnosis. 2025; 1.

Chiang, S; Yang, L; Akeno, N; Owsley, E; de Jesus, A; Goldbach-Mansky, R; Marsh, R; Bleesing, J. Validation of an Interferon Type I Score Test on the Nanostring nCounter Platform. 2025; 1.

Chiang, SC C; Yang, L; Owsley, E; Husami, A; Akeno, N; Cobb, C; Hartog, NL; Elizalde, A; Seroogy, CM; Blanchard-Rohner, G; Marsh, R; Bleesing, J; Jordan, MB; Marwaha, AK. Lipopolysaccharide-responsive and beige-like anchor protein (LRBA) functional deficiency caused by biallelic LRBA missense variants characterized by Evans syndrome or colitis. Journal of Allergy and Clinical Immunology. 2025; 156:270-278.

Choi, J; Koo, J. Protein-Protein Interactions of Odorant and G Protein-Coupled Receptors: A BRET Analysis Approach. Methods in molecular biology (Clifton, N.J.). 2025; 2915:161-168.

Choi, J; Koo, J. Yellow Fluorescent Protein Quenching Assay for Analyzing Odorant Receptor Activity. Methods in molecular biology (Clifton, N.J.). 2025; 2915:169-177.

Chowdhury, I; Jakobsen, ER; Krupski, M. A strongly degenerate fully nonlinear mean field game with nonlocal diffusion. Journal of Differential Equations. 2025; 440:113436.

Cook, E; Haacker, L; Chandra, S; Jordan, MB; Verkamp, B; McCarthy, L; Rotz, SJ; Hammoud, MS; Pariury, H; McKeone, D; Kumar, A. EBV-Associated T/NK-LPD Manifesting As HLH Cured By Nivolumab and Emapalumab, Avoiding the Need for Allogeneic HCT. Transplantation and Cellular Therapy. 2025; 31:s43.

Cook, E; Langenberg, L; Luebbering, N; Ibrahimova, A; Myers, KC; Sabulski, A; Dandoy, C; Lake, K; Ziady, A; Lane, A; Webster, A; Abdullah, S; Jodele, S; Davies, SM. Oxidative Stress Early After Hematopoietic Stem Cell Transplant. Transplantation and Cellular Therapy. 2025; 31:135.e1-135.e10.

Cook, E; Schulert, G; Grom, A; Towe, C; Burg, G; Marsh, R; Chandra, S. Experience with T Cell–Depleted Allogeneic HSCT for Refractory sJIA Associated with Lung Disease. 2025; 1.

Dandoy, CE; Auletta, JJ; Badia, P; Bidgoli, A; Daraiseh, NM; DeSalvo, AM; Diaz, J; Davies, SM; Demmel, K; Cook, E; Salem, BM; Snyder, A; Juckett, M; Hartley, D. Engraft: A Collaborative Learning Health Network for Enhanced Transplant and Cellular Therapy Outcomes. Transplantation and Cellular Therapy. 2025; 31:123-134.

Davies, SM; Grimley, MS; Shrestha, A; Shova, A; Asnani, M; Kent, M; Sayani, F; Quinn, CT; Niss, O; Lutzko, CM; Witting, S; Latham, T; Bushman, FD; Malik, P. Gene Therapy with Reduced-Intensity Conditioning for Sickle Cell Disease. Transplantation and Cellular Therapy. 2025; 31:s2-s3.

Dávila Saldaña, BJ; Schultz, KR; Ramgopal, A; Boiko, JR; Beebe, K; Carpenter, PA; Chan, SS; Paczesny, S; Aguayo-Hiraldo, P; Cuvelier, GD E; Rotz, SJ; Duncan, CN; Williams, KM. Pediatric Transplant and Cellular Therapy Consortium RESILIENT Conference on Pediatric Chronic Graft-versus-Host Disease Survivorship after Hematopoietic Cell Transplantation: Part II. Organ Dysfunction and Immune Reconstitution Considerations for Children with Chronic Graft-versus-Host Disease after Hematopoietic Cell Transplantation. Transplantation and Cellular Therapy. 2025; 31:347.e1-347.e17.

Dei-Adomakoh, YA; Segbefia, CI; Latham, TS; Lane, AC; Dzefi-Tettey, K; Amissah-Arthur, K; Corquaye, O; Korang, L; Mensah, E; Ekpale, P; Seedah, D; Stuber, SE; Smart, LR; Ware, RE. Hydroxyurea for Children and Adults with Hemoglobin SC Disease. 2025; 4:EVIDoa2400402.

Djassemi, N; Kinoshita, H; Maghzian, N; Datar, A; Joy, E; McCann, C; Shibli, A; Saldana, BD; Hoq, F; Hanley, PJ; Pulsipher, MA; Bollard, CM; Keller, MD. Outcome Analysis Post Virus-Specific T Cell Therapy for the Treatment of Adenoviremia in Immunocompromised Pediatric Patients. Transplantation and Cellular Therapy. 2025; 31:s221-s222.

Drozdov, D; Luo, X; Marsh, RA; Abraham, RS; Ebens, CL. Relevance of Recent Thymic Emigrants Following Allogeneic Hematopoietic Cell Transplantation for Pediatric Patients with Inborn Errors of Immunity. Transplantation and Cellular Therapy. 2025; 31:265.e1-265.e12.

Durkee-Shock, J; Cohen, A; Maghzian, N; Pezzella, G; Jensen-Wachspress, M; Hostal, A; Barton, K; Gangler, K; Dávila Saldaña, BJ; Chaimongkol, N; Gonzalez, C; Notarangelo, LD; Green, KY; Keller, MD. Reconstitution of Norovirus-Specific T-Cell Responses Following Hematopoietic Stem Cell Transplantation in Patients With Inborn Errors of Immunity and Chronic Norovirus Infection. The Journal of Infectious Diseases. 2025; 231:773-783.

Fidler, AL; O'Connor, G; Beebe, DW; Wang, YZ M; Crosby, LE; Dandoy, CE. How to Improve the Sleep of Hospitalized Pediatric Patients: Family and Staff Focus Groups. Transplantation and Cellular Therapy. 2025; 31:586.e1-586.e11.

Fragneau, R; Fraitag, S; Kemps, PG; Hélias-Rodzewicz, Z; Roy, S; Bonsang, B; Bartlett, AL; Dhar, S; Jankofsky, M; Zlocha, J; Donadieu, J; Borkhardt, A; Picarsic, JL; Emile, JF. NTRK1-rearranged histiocytosis: clinicopathologic and molecular features. Blood Advances. 2025; 9:3617-3628.

Galletta, TJ; Benoit, SW; Markham, J; Pillay-Smiley, N; Queen, K; Graham, RT. Elevated Bromide Levels Due to Tazemetostat Therapy Treated With Salt and Water Supplementation in Two Children With Atypical Teratoid Rhabdoid Tumor. Pediatric Blood and Cancer. 2025; 72:e31803.

Ginocchio, MP; Gutarra, ME; Ramos, KN; Shah, R; Pandey, M; Ghalehsari, N; Davies, SM; Auletta, DJ J; Hall, AG; Arteaga, AG. Understanding Diversity: An ASTCT-NMDP Access Initiative Survey of the Hematopoietic Cell Transplant and Cellular Therapy Nonphysician Workforce. Transplantation and Cellular Therapy. 2025; 31:s343-s344.

Ginocchio, MP; Ramos, KN; Gutarra, ME; Ghalehsari, N; Pandey, M; Shah, R; Davies, SM; Auletta, DJ J; Arteaga, AG; Hall, AG. Physician Workforce Diversity in the Hematopoietic Cell Transplant and Cellular Therapy Ecosystem: An ASTCT-NMDP Access Initiative Survey. Transplantation and Cellular Therapy. 2025; 31:s361.

Grassia, KL; Diseroad, E; Jodele, S; Dandoy, DC E; Towe, C; Davies, SM; Sabulski, DA. Managing Diffuse Alveolar Hemorrhage in Pediatric HSCT with Inhaled and Intrabronchial Therapy: A Case Series of Targeted Hemostatic Intervention. Transplantation and Cellular Therapy. 2025; 31:s153.

Grimley, M; Davies, SM; Shrestha, A; Shova, A; Asnani, M; Kent, M; Sayani, F; Quinn, CT; Niss, O; Lutzko, C; Witting, S; Latham, T; Bushman, FD; Malik, P. Lentiviral gene therapy with reduced-intensity conditioning for sickle cell disease: a phase 1/2 trial. Nature Medicine. 2025; 31:2204-2212.

Hahn, TE; Zhao, Q; Miller, EG; Elder, P; Langenberg, L; Davies, SM; Bejanyan, N; Vasu, S. Incidence of Transplant-Associated Thrombotic Microangiopathy (TA-TMA) Is Not Lowered By Reduction of Acute GvHD (aGvHD) in Patients Receiving Post-Transplant Cyclophosphamide (PTCy) GvHD Prophylaxis: A Report from the MIDAS (Microangiopathy, Endothelial Damage in Adults undergoing Stem cell transplantation) Consortium. Transplantation and Cellular Therapy. 2025; 31:s282.

Haney, M; Ashraf, A; Lake, KE; Strecker, L; Myers, KC; Towe, C; Walkup, L; Woods, J; Edwards, SL; Cooper, R; Goldfarb, SB; Davies, SM; Koo, J; Groups, T. Community respiratory viruses are generally welltolerated in hematopoietic stem cell transplant recipients: a brief report from the TRANSPIRE study. Haematologica: the hematology journal. 2025; 110:1882-1886.

He, CB; Pham, D; Kronenfeld, RS; Rosenberg, A; Ardente, J; Dhir, A. The Importance of Next-Generation Sequencing in Identifying Immunohistochemically Ambiguous Pediatric Sarcomas. Editor, Mayordomo JI. Case Reports in Oncological Medicine. 2025; 2025:9926653.

Huber, J; Auletta, DJ J; Cook, E; Culbertson, C; Diaz, J; Fitch, T; Flesch, L; French, K; Jaglowski, S; Jodele, S; Snyder, AJ; Hartley, D; Dandoy, DC E; Liang, DW H. Establishing the Engraft Multi-Center Tri-Use Registry. Transplantation and Cellular Therapy. 2025; 31:s529-s530.

Hudda, DZ; Lawhorn, E; Mani, B; Badia, P; Frias, O; Myers, KC; Howell, JC; Burns, K. Longitudinal Outcomes of Fertility Potential in Female Pediatric and Young Adult Allogeneic Hematopoietic Stem Cell Transplant Survivors. Transplantation and Cellular Therapy. 2025; 31:s98.

Hudda, DZ; Schoettler, ML; Rotz, SJ; Kapadia, M; Lehmann, LE; Freedman, JL; Pater, L; Weiss, B; Badia, P; Davies, SM; Mormann, M; Desai, A; Webster, A; Dandoy, DC E. Acute Toxicities and Early Outcomes of Tandem Autologous Stem Cell Transplantation in Pediatric High-Risk Neuroblastoma: A Multicenter Study. Transplantation and Cellular Therapy. 2025; 31:s93-s94.

Hudda, Z; Flannery, A; Dillhoff, P; Webster, K; Jacobs, J; Strong, S; Detzel, J; Davies, SM; Khandelwal, P. Chronic Graft-Versus-Host Disease Adversely Impacts School Performance in Children and Young Adults. Transplantation and Cellular Therapy. 2025; 31:99.e1-99.e11.

Hussain, M; Nagarsheth, N; Jones, J; Bleesing, J; Chandra, S; Marsh, R; Dansereau, C; O'Donnell, M; Silva, O; Kerwin, B; De Ravin, SS; Prockop, S; Williams, D; Pai, S. A Novel Dominant Negative Variant in IL2RG Gene that Failed to Be Corrected by Lentiviral Gene Therapy. 2025; 1.

Hyeong, J; Koo, J; Rim, M; Wi, Y; Ko, H; Yu, D; Kim, S; Kim, N; Yoo, MJ; Jeong, K. Stretchable Heat Transfer Eco-Materials: Mesogen Grafted NR-Based Nanocomposites with High Thermal Conductivity and Low Dielectric Constant. Small. 2025; 21:e2406066.

Ibrahimova, A; Ashraf, A; Klink, G; Teusink-Cross, A; Davies, SM; Khandelwal, P. Single Center Experience of Belumosudil in Children < 12 Years, Adolescents and Young Adults. Transplantation and Cellular Therapy. 2025; 31:s305-s306.

Ibrahimova, A; Khoury, R; Jodele, S; Grimley, M; Davies, SM; Khandelwal, P. Abatacept for acute graft versus host disease prophylaxis in children with sickle cell disease patients undergoing HLA identical sibling hematopoietic stem cell transplantation. Bone Marrow Transplantation. 2025; 60:1102-1107.

Ibrahimova, A; Luebbering, N; Langenberg, L; Abdullah, S; Strecker, L; Lake, KE; Lane, A; Webster, A; Myers, KC; Jodele, S; Davies, SM. Kinetics of DNases after hematopoietic stem cell transplant. 2025; 2:100055.

Jodele, S; Gavriilaki, E. Translating biomarker insights into practice: a path forward in TA-TMA management. Frontiers in Medicine. 2025; 12:1550365.

Josephson, M; Boas, H; Freedman, J; Young, LR; Goldfarb, SB; Robinson, PD; Towe, C; Gaffin, JM; Wong, W; Koo, J; Lane, A; Davies, SM; Mc Donough, J; Allen, JL. Intrabreath Oscillometry (IBO) vs. Spectral Oscillometry (SO) in Detecting Respiratory Disease in Patients Undergoing Hematopoietic Stem Cell Transplantation (HSCT). American Journal of Respiratory and Critical Care Medicine. 2025; 211:a5118.

Khandelwal, P; Fish, JD; Gorfinkel, L; Guilcher, GM T; Howell, J; Nishitani, M; Nuechterlein, B; Obeng, E; Shah, AJ; Cuvelier, GD E; Rotz, S; Williams, KM; Duncan, CN. Pediatric Transplant and Cellular Therapy Consortium RESILIENT Conference on Pediatric Chronic Graft-versus-Host Disease Survivorship after Hematopoietic Cell Transplantation: Part III. Long-Term Impact of Chronic Graft-versus-Host Disease on Endocrinologic, Cardiovascular, and Metabolic Outcomes in Survivors of Pediatric Hematopoietic Cell Transplantation. Transplantation and Cellular Therapy. 2025; 31:297.e1-297.e15.

Khoury, R; Jordan, M; Bleesing, J; Kumar, A; Saldana, BD; Verkamp, B; Davies, S; Marsh, R; Chandra, S. Addition of Thiotepa to Alemtuzumab, Fludarabine, and Melphalan Reduced-Intensity Conditioning Reduces Secondary Graft Failure in Allogeneic HSCT for Inborn Errors of Immunity. 2025; 1.

Konduri, M; Boe, D; Yazigi, N; Khan, K; Ward, BR; Saldana, BD; Cavener, D; Kallakury, B; Kroemer, A; Matsumoto, C; Fishbein, T; Ekong, UD. Wolcott-Rallison syndrome - crosstalk between PERK- EIF2A and type II interferon signaling. European Journal of Medical Genetics. 2025; 76:105022.

Koo, DJ; Lake, KE; Langenberg, L; Anderson, J; Edwards, MS L; Teusink-Cross, A; Romick-Rosendale, L; Sabulski, DA; Jodele, S; Davies, SM. Pravastatin Prophylaxis Is Safe and Feasible in Children and Young Adults Undergoing Allogeneic HSCT: A Prospective, Single Arm Cohort Study. Transplantation and Cellular Therapy. 2025; 31:s153-s154.

Koo, DJ; Miller, E; O'Conner, A; Campbell, KM; Grompe, M; Myers, KC; Mehta, PA; Davies, SM. Beyond Graft-Vs-Host Disease: The Role of Cellular Senescence in Persistent Liver Injury in Fanconi Anemia after HSCT. Transplantation and Cellular Therapy. 2025; 31:s311-s312.

Koo, DJ; Webster, A; Dandoy, DC E; Jodele, S; Davies, SM; Sabulski, DA. The Tell-Tale Heart: A Cytokine Storm Story of Pericardial Effusions after HSCT. Transplantation and Cellular Therapy. 2025; 31:s137.

Koo, DJ; Webster, A; Myers, KC; Davies, SM; Davies, SM; Sabulski, DA. Transcriptomic Alterations and Clonal Evolution Identifies a Pre-Emptive Indication for Hematopoietic Stem Cell Transplant in Fanconi Anemia. Transplantation and Cellular Therapy. 2025; 31:s308-s309.

Koo, J; Cooper, R; Edwards, SL; Lane, A; Loveless, SK; Strecker, L; Lake, KE; Myers, KC; Towe, C; Patti, J; Li, M; Goldfarb, SB; Woods, JC; Davies, SM. High Prevalence of Abnormal Baseline Lung Function in Pediatric and Young Adult Hematopoietic Stem Cell Transplant Recipients: A Report from the TRANSPIRE Study. Pediatric Blood and Cancer. 2025; e31916.

Kusoski, CL; Mehta, PA; Markham, J; Murphy, M; Teusink-Cross, A. Higher Dose Intravenous Posaconazole Is Safe and Necessary for Achievement of Therapeutic Targets and Prevention of Infections in Pediatric Hematopoietic Stem Cell Transplant Patients. Transplantation and Cellular Therapy. 2025; 31:s546.

Langenberg, L; Abdullah, S; Lies, E; Benoit, SW; Ramos, KN; Jodele, S; Davies, SM; Sabulski, DA. Urine Kidney Injury Biomarkers Predict TMA Risk in Pediatric HSCT Recipients. Transplantation and Cellular Therapy. 2025; 31:s314.

Langenberg, L; Jodele, S; Davies, SM; Sabulski, DA. Supar Is a Novel and Powerful Biomarker of TMA and Kidney Injury after HSCT. Transplantation and Cellular Therapy. 2025; 31:s313-s314.

Lichtenstein, DA; Sridharan, A; Khoury, R; Grimley, MS; Rubinstein, JD; Lutzko, CM; Wang, YM. Effect of Clinically Relevant Immunosuppressants on Viral Specific T-Cell (VST) in Vitro Function. Transplantation and Cellular Therapy. 2025; 31:s509-s510.

Liu, B; Sajiki, Y; Littlefield, N; Hu, Y; Stuart, WD; Sridharan, A; Cui, X; Siefert, ME; Araki, K; Ziady, AG; Shi, D; Whitsett, JA; Maeda, Y. PBAE-PEG-based lipid nanoparticles for lung cell-specific gene delivery. Molecular Therapy. 2025; 33:1154-1165.

Macaraeg, M; Baker, E; Handorf, E; Matt, M; Brunner, H; Grom, AA; Henrickson, M; Huggins, J; Zhang, W; Lee, P; Marsh, R; Schulert, GS. Clinical, Immunologic, and Genetic Characteristics in Patients With Syndrome of Undifferentiated Recurrent Fevers. Arthritis and Rheumatology. 2025; 77:596-605.

Maier, S; Auletta, DJ J; Badia, P; Cook, E; Craddock, JA; Culbertson, C; Daraiseh, N; Davies, SM; DeSalvo, AM; Diaz, J; Nishitani, M; Snyder, AJ; Dandoy, DC E; Parker, L. Establishing a Quality Improvement Education Platform in the Engraft Learning Network. Transplantation and Cellular Therapy. 2025; 31:s501.

Manjrekar, P; Sabulski, DA; Lies, E; Dandoy, DC E; Davies, SM; Laskin, B; Jodele, S. The HCT Protein Shake: Moderate and Severe Proteinuria Are Specific to TA-TMA. Transplantation and Cellular Therapy. 2025; 31:s145.

Maron, G; Boeckh, MJ; Papanicolaou, G; Gomez, C; Prasad, V; Dara, J; Elgarten, C; Kumar, M; Wynn, R; Lion, T; Fukushima, K; Maher, R; Azie, N; Grimley, M. P-103. Adenoviremia Clearance Following Treatment with Intravenous (IV) Brincidofovir (BCV) in Immunocompromised Patients is Associated with Positive Clinical Disease Response: Preliminary Outcomes from the ATHENA Phase IIa Study. Open Forum Infectious Diseases. 2025; 12:ofae631.310.

Marsh, R; Khoury, R; Mizuno, K; Hosawi, A; Cottrell, C; Nguyen, E; Landon, B; Chandra, S; Jordan, M; Kumar, A; Bleesing, J; Davies, S; Moore, C; Mehta, P. Precision Alemtuzumab Dosing Results in Day 0 Target Range Achievement in 80% of IEI Patients and Minimizes Risks of GVHD, Clinically Significant Mixed Chimerism, and Secondary Graft Failure. 2025; 1.

Marsh, RA; Bleesing, JJ; Chiang, SC C. Diagnostic testing for hemophagocytic lymphohistiocytosis. Journal of Immunological Methods. 2025; 537:113816.

Matt, MG; Drozdov, D; Bendstrup, E; Glerup, M; Hauge, EM; Masmas, T; Schneider, EC; Zeilhofer, UB; Abu-Arja, RF; Driest, KD; Chandra, S; Grom, A; Schulert, GS; Marsh, RA. Allogeneic haematopoietic stem-cell transplantation for children with refractory systemic juvenile idiopathic arthritis and associated lung disease: outcomes from an international, retrospective cohort study. The Lancet. Rheumatology. 2025; 7:e243-e251.

McCormack-Spivey, S; Laskin, B; Seif, AE; Blackard, JT; Odegard, E; Kleiboeker, S; Jodele, S; Bourgeois, T; Zee, J; Davies, SM; Sabulski, DA. The First Prospective Screening Study of BK Polyomavirus (BKPyV) Hemorrhagic Cystitis after HSCT. Transplantation and Cellular Therapy. 2025; 31:s513-s514.

McCormack-Spivey, S; Sabulski, DA; Davies, SM; Chandra, S. Defining and Assessing Poor Graft Function after Allogeneic HSCT in Children and Young Adults. Transplantation and Cellular Therapy. 2025; 31:s317-s318.

McCormack-Spivey, S; Strecker, L; Webster, A; Davies, SM; Sabulski, DA. Plasma LILRA6 Levels Influence BK Polyomavirus Cystitis after HSCT. Transplantation and Cellular Therapy. 2025; 31:s514-s515.

Mehta, PA; Nelson, A; Loveless, S; Lane, A; Fukuda, T; Teusink-Cross, A; Elder, D; Lagory, D; Miller, E; Cancelas, JA; Edwards, S; Chihanga, T; Wells, SI; Davies, SM. Phase 1 study of quercetin, a natural antioxidant for children and young adults with Fanconi anemia. Blood Advances. 2025; 9:1927-1939.

Merli, P; Jodele, S; Cook, E; Myers, KC; Lane, A; Ryhänen, S; Cefalo, MP; Quagliarella, F; Davies, SM; Teusink-Cross, A; Kohorst, M; Corsetti, T; Locatelli, F; Sabulski, A. Emapalumab for the Treatment of Immune-Mediated Graft Failure after HSCT. Bone Marrow Transplantation. 2025; 60:406-411.

Meyer, R; Orndorff, L; Engel, H; Hoback, P; Spivey, S; Mikut, K; Spears, K; Clark, A; Sarver, S; Dandoy, DC E. Nurse Driven Central Line Rounding Utilized to Improve Bone Marrow Transplant Patient Outcomes: An Update. Transplantation and Cellular Therapy. 2025; 31:s451.

Mizuno, K; Teusink-Cross, A; Sabulski, DA; Davies, SM; Jodele, S. Unraveling the Challenges of Non-Responders to the Eculizumab Treatment with High-Risk Hematopoietic Stem Cell Transplant-Associated Thrombotic Microangiopathy (TA-TMA). Transplantation and Cellular Therapy. 2025; 31:s542-s543.

Murphy, CR; Liu, C; Courter, J; Griffin, C; Scaggs Huang, F; Miller-Handley, H; Grimley, MS; Danziger-Isakov, L; Otto, WR. Receipt of Fluoroquinolone Prophylaxis is not Associated With Development of Vancomycin-Resistant Enterococcus Colonization During Pediatric Hematopoietic Cell Transplantation. Journal of the Pediatric Infectious Diseases Society. 2025; 14:piaf010.

Myers, KC; Davies, SM; Lutzko, C; Wahle, R; Grier, DD; Aubert, G; Norris, K; Baird, DM; Koga, M; Ko, AC; Amano, T; Amano, M; Yu, H; Ko, MS H. Clinical Use of ZSCAN4 for Telomere Elongation in Hematopoietic Stem Cells. 2025; 4:EVIDoa2400252.

Nath, K; Zhang, MJ; Bye, M; Abid, MB; Benjamin, C; Betts, B; Bhatt, NS; Bolaños, EA; Bolon, YT; Gadalla, SM; Shaw, BE; Spellman, SR; Choe, H; Shaffer, BC. Transplant outcomes using older matched sibling donors compared with young alternative donors: a CIBMTR analysis. Blood Advances. 2025; 9:3469-3478.

Nayak, RC; Emberesh, S; Trump, LR; Wellendorf, AM; Singh, AK; Korkmaz, B; Horwitz, MS; Myers, KC; Kalfa, TA; Lutzko, CM; Cancelas, JA. G-CSF resistance of ELANE-mutant neutropenia depends on SERF1-containing truncated-neutrophil elastase aggregates. The Journal of Clinical Investigation. 2025; 135:e177342.

Naymagon, L; Roehrs, P; Hermiston, M; Connelly, J; Bednarski, J; Boelens, J; Chandrakasan, S; Dávila Saldaña, B; Henry, MM; Satwani, P; Teachey, D; Behrens, EM; Canna, SW; Kumar, A. Perspectives on the current diagnostic and treatment paradigms in secondary hemophagocytic lymphohistiocytosis (HLH). Orphanet Journal of Rare Diseases. 2025; 20:200.

Neidemire-Colley, L; Zhao, Q; Miller, EG; Langenberg, L; Elder, P; Hahn, TE; Bejanyan, N; Davies, SM; Ranganathan, P; Vasu, S. Soluble Fms-like Tyrosine Kinase-1 (sFlt-1) As a Clinical Biomarker for Individual Susceptibility to Post-Transplant Complications: A Report from the MIDAS Consortium. Transplantation and Cellular Therapy. 2025; 31:s26-s27.

Nguyen, TH; Satwani, P; Kumar, D; Kapoor, U; Malik, S; Prince, C; Montminy, T; Smiley, K; Martinez, M; Goldner, D; Fazlollahi, L; Rytting, HB; Romero, R; Chandrakasan, S. Systemic T-cell activation and IFN-γ activity in indeterminate severe hepatitis are reminiscent of hemophagocytic lymphohistiocytosis: Implications for T-cell- and IFN-γ-directed therapies. Journal of Allergy and Clinical Immunology. 2025; 155:199-212.

Nieves, RM; Latham, T; Marte, N; Berges, M; Sánchez, LM; Urcuyo, G; Florencio, C; Gonzalez, C; del Villar, P; Chen, S; Schultz, WH; Lane, AC; Mena, R; Ware, RE. Stroke prevention in Hispanic children with sickle cell anemia: the SACRED trial. Blood Advances. 2025; 9:1791-1800.

Perales, MA; Riches, M; He, N; Martens, MJ; Chemaly, RF; Dandoy, CE; Hill, JA; Diaz, MA; Hashmi, S; Prockop, S; Lazarus, HM; Beitinjaneh, AM; Hildebrandt, GC; Auletta, JJ; Szabolcs, P. Delayed T-cell recovery after hematopoietic cell transplantation is associated with decreased overall survival in adults. Blood Advances. 2025; 9:3502-3517.

Pham, D; Vera, A; He, CB; Kronenfeld, RS; Trillo, A; Ghosh, T; Garcia, J; Tekin, A; Mohan, P; Portelance, L; Alperstein, W; Dhir, A. Novel Use of Bland Trans-Arterial Embolization for Hepatoblastoma: A Case Report. Pediatric Transplantation. 2025; 29:e70121.

Phelan, R; Rotz, S; Dandoy, CE; Auletta, JJ; Badia, P; Bhatt, NS; Ballard, SA; Blacken, R; Daraiseh, NM; Desmond, C; Pai, A; Tarquini, S; Fitch, TJ; Hartley, D. Multicenter Study on Caregiver Experiences in Pediatric Hematopoietic Stem Cell Transplantation: Part II. Treatment Challenges, Communication Barriers, and Caregiver-Driven Approaches to Mitigation. Transplantation and Cellular Therapy. 2025; 31:590.e1-590.e16.

Potter, A; Sharma, N; Patel, K; Qureshi, M; Khan, M; Wallace, C; Ziady, A; Morales, D; Hayes, D. (276) Gene Expression Alterations in Lung Allografts with ACR and After Treatment Compared to Never ACR. The Journal of Heart and Lung Transplantation. 2025; 44:s140.

Potter, A; Sharma, N; Patel, K; Qureshi, MR; Khan, M; Wallace, C; Ziady, A; Ashfaq, A; Moore, C; Hayes, D. Persisting Inflammatory and Fibrotic Gene Signatures Linking Acute Cellular Rejection to Chronic Lung Allograft Dysfunction. American Journal of Transplantation. 2025; 25:s823-s824.

Potter, A; Sharma, N; Wallace, C; Ziady, A; Moore, C; Morales, D; Hayes, D. (750) Single Cell Technology Shines LIGHT on Acute Lung Allograft Dysfunction. The Journal of Heart and Lung Transplantation. 2025; 44:s355.

Power-Hays, A; Namazzi, R; Dong, M; Kazinga, C; Kato, C; Aliwuya, S; McElhinney, K; Conroy, AL; Lane, A; John, C; Vinks, AA; Latham, T; Opoka, RO; Ware, RE. The feasibility of pharmacokinetic-based dosing of hydroxyurea for children with sickle cell anaemia in Uganda: Baseline results of the alternative dosing and prevention of transfusions trial. British Journal of Clinical Pharmacology. 2025; 91:1865-1872.

Power-Hays, A; Namazzi, R; Dong, M; Kazinga, C; Kato, C; Aliwuya, S; McElhinney, K; Conroy, AL; Lane, A; John, C; Vinks, AA; Latham, T; Opoka, RO; Ware, RE. The feasibility of pharmacokinetic-based dosing of hydroxyurea for children with sickle cell anaemia in Uganda: Baseline results of the alternative dosing and prevention of transfusions trial. British Journal of Clinical Pharmacology. 2025; 91:1865-1872.

Power-Hays, A; Namazzi, R; Kato, C; McElhinney, KE; Conroy, AL; Hume, H; John, C; O'Hara, SM; Stuber, SE; Lane, A; Latham, TS; Opoka, RO; Ware, RE. Pharmacokinetic-Guided Hydroxyurea to Reduce Transfusions in Ugandan Children with Sickle Cell Anemia: Study Design of the Alternative Dosing And Prevention of Transfusions Trial. Acta Haematologica. 2025; 148:208-219.

Ramos, KN; Ginocchio, MP; Gutarra, ME; Ghalehsari, N; Pandey, M; Shah, R; Davies, SM; Auletta, DJ J; Arteaga, AG; Hall, AG. Perception and Reality of Racial and Ethnic Workforce Diversity in the U.S HCT/CT Workforce: Results from the ASTCT-NMDP Access Initiative Survey. Transplantation and Cellular Therapy. 2025; 31:s342.

Ramos, KN; Zee, J; Sabulski, DA; Laskin, B; Blackard, JT; Langenberg, L; Dandoy, DC E; Davies, SM; Jodele, S. Pre-Transplant Complement Activation and Transplant-Associated Thrombotic Microangiopathy (TA-TMA) across Diagnostic Groups. Transplantation and Cellular Therapy. 2025; 31:s25-s26.

Reed, HD; Do, H; Weller, E; Harris, MH; Reilly, CR; Tsai, HK; Farrar, JE; Lau, BW; Pommert, L; Gamper, C; Cheng, L; Malsch, M; Myers, K; Shimamura, A. Lymphoid malignancies in patients with Shwachman-Diamond syndrome. Blood. 2025; 145:2528-2532.

Reinert, S; Benoit, SW; Nagarajan, R. Long-term kidney outcomes in survivors of Wilms tumor: a single-center retrospective cohort study. Pediatric Nephrology. 2025; 40:1603-1611.

Sabulski, DA; Webster, A; Langenberg, L; Luebbering, N; Dandoy, DC E; Koo, DJ; Jodele, S; Davies, SM. TA-TMA Evolution and Individual Susceptibility at the Proteome Level. Transplantation and Cellular Therapy. 2025; 31:s133.

Sampson, M; Parker, L; Dandoy, DC E; Auletta, DJ J; Chapman, LR M; Cook, E; Craddock, J; Culbertson, C; Daraiseh, N; Diaz, J; Snyder, AJ; Staton, S; Wall, SA; Badia, P. Variation in Central Venous Catheter Practices and Complications after Stem Cell Transplant: A Multi-Center Survey of the Engraft Learning Network. Transplantation and Cellular Therapy. 2025; 31:s535-s536.

Samra, S; Cook, E; Wilson, J; Sharma, M; Golding, L; Yao, DT; Marsh, RA; Turvey, SE. STAT6 gain-of-function disease: p.D519N is a new disease-causing variant that responds well to dupilumab treatment. Journal of Allergy and Clinical Immunology: Global. 2025; 4:100494.

Schumacher, DJ; Michelson, C; Winn, A; Henry, D; O’Connor, M; Li, ST T; Blair, RJ; Velazquez-Campbell, M; Kihlstrom, MJ; Borman-Shoap, E; Alba-Sandoval, M; Burrows, HL; Stewart, DA; Scheurer, JM. Graduating Residents' Readiness for Unsupervised Practice. Pediatrics. 2025; 155:e2024070307.

Sharma, A; O'Brien, MM; Phillips, CL; Schultz, KR; Mehta, PA; Kebriaei, P; Vandendries, E; Dorman, S; Jiang, W; Zhang, F; Asomaning, K; Zhang, M; De Lima, MJ G; Marks, DI; Saber, W. Sinusoidal obstruction syndrome and other outcomes in pediatric patients with acute lymphoblastic leukemia who received inotuzumab ozogamicin before hematopoietic cell transplantation. Journal of Clinical Oncology. 2025; 43.

Snyder, AJ; Strecker, L; Langenberg, L; Davies, SM; Koo, DJ; Elder, P; Zhao, Q; Bejanyan, N; Hahn, TE; Vasu, S. Pre-Transplant Endothelial Activation May Increase Individual Susceptibility Transplant-Associated Thrombotic Microangiopathy in Adults: A Report from the MIDAS Consortium. Transplantation and Cellular Therapy. 2025; 31:s133-s134.

Spears, K; Meyer, R; Goodin, CS; Kusnier, K; Nell, O; Pearson, P; Sanchez, M; Sarver, S; Haslam, D; Dandoy, DC E; Davies, SM; Badia, P. Scrubbing Olympics: Next Steps. Transplantation and Cellular Therapy. 2025; 31:s489.

Strecker, L; Webster, A; Luebbering, N; Laskin, B; Seif, AE; Blackard, JT; Jodele, S; Odegard, E; Davies, SM; Sabulski, DA. The Novel Role of Pilra in BK Polyomavirus Cystitis after HSCT. Transplantation and Cellular Therapy. 2025; 31:s167.

Taggart, CB; Bota, KE; Young, K; Wall, J; Davies, SM; Dandoy, DC E; Ramos, KN. Inbody Assessments Reveal Important Changes in Body Mass Composition during HCT. Transplantation and Cellular Therapy. 2025; 31:s146.

Takahashi, T; Watkins, B; Bratrude, B; Neuberg, D; Hebert, K; Betz, K; Yu, A; Choi, SW; Davis, J; Duncan, C; Horan, JT; Langston, A; Kean, LS; Qayed, M. The Adverse Event Landscape of Stem Cell Transplant: Evidence for AGVHD Driving Early Transplant Associated Toxicities. Transplantation and Cellular Therapy. 2025; 31:109.e1-109.e13.

Thakar, MS; Logan, BR; Liu, X; Dunn, E; Chandra, S; Ebens, CL; Buckley, RH; O'Reilly, RJ; Heimall, JR; Kapadia, M; Cowan, MJ; Puck, J; Pai, S; Haddad, E. The Role of Second Hematopoietic Cell Transplantation (HCT2) in Patients with Severe Combined Immunodeficiency (SCID): A Report from the Primary Immune Deficiency Treatment Consortium (PIDTC). Transplantation and Cellular Therapy. 2025; 31:s92-s93.

Todd, K; Hogue, SJ; Tweddell, JS; Reagor, JA; Mullins, E; Block, MG; Rosenfeldt, L; Francisco, B; Jodele, S; Sharma, BK; Lane, A; Slusher, C; Kharnaf, M; Morales, DL S; Palumbo, JS. Hemostatic derangements associated with cardiopulmonary bypass predict outcomes in pediatric patients undergoing corrective heart surgery. Journal of Thrombosis and Haemostasis. 2025; 23:492-503.

Tomomasa, D; Nishimura, M; Ohya, A; Tanita, K; Wakatsuki, R; Watanabe, R; Miyamoto, S; Hoshino, A; Kamiya, T; Isoda, T; Takagi, M; Morio, T; Marsh, RA; Kanegane, H. Comprehensive flow cytometry-based diagnosis of XIAP deficiency. Clinical and Experimental Immunology. 2025; 219:uxaf020.

Urrego, F; Stevens, C; Myers, K; Josephson, M; Silva Carmona, MD J; Gaffin, JM; Abts, MF; Koo, J; Wong, W; Towe, C; Allen, JL; Davies, SM; Goldfarb, SB. Home Spirometry for Early Identification of Pulmonary Dysfunction After Hematopoietic Stem Cell Transplant in the Transpire Research Study. American Journal of Respiratory and Critical Care Medicine. 2025; 211:a7235.

Vasu, S; Zhao, Q; Miller, EG; Elder, P; Langenberg, L; Cataland, S; M Davies, S; Bejanyan, N; Hahn, T. High incidence of severe TA-TMA increases mortality in adult allogeneic transplant recipients: a prospective MIDAS Consortium study. Blood. 2025; 146:638-646.

Vasu, S; Zhao, Q; Miller, EG; Habib, A; Elder, P; Davies, SM; Bejanyan, N; Hahn, TE. Pre-HCT Creatinine and Early Post-HCT Changes in Creatinine and Blood Pressure Associate with Severe Transplant Associated Thrombotic Microangiopathy (TA-TMA): A Report from the MIDAS (Microangiopathy, Endothelial Damage in Adults undergoing Stem cell transplantation) Consortium. Transplantation and Cellular Therapy. 2025; 31:s149.

Venkatasubramanian, M; Schwartz, L; Ramachandra, N; Bennett, J; Subramanian, KR; Chen, X; Gordon-Mitchell, S; Fromowitz, A; Pradhan, K; Shechter, D; Grimes, HL; Starczynowski, DT; Verma, A; Salomonis, N. Splicing regulatory dynamics for precision analysis and treatment of heterogeneous leukemias. Science Translational Medicine. 2025; 17:eadr1471.

Verkamp, B; Dandoy, DC E; Badia, P; Haslam, D; Davies, SM; Khandelwal, P. Characterizing the Gut Microbiome in Pediatric Patients Undergoing Hematopoietic Cell Transplant for a Non-Malignant Diagnosis. Transplantation and Cellular Therapy. 2025; 31:s316-s317.

Verkamp, B; Soliman, A; Davies, SM; Krupski, C. Influence of the Incorporation of a Muslim Chaplain on Medical Decision-Making in a Pediatric Hematopoietic Cell Transplant Program. Transplantation and Cellular Therapy. 2025; 31:s355.

Voit, RA; Liao, X; Caulier, A; Antoszewski, M; Cohen, B; Armant, M; Lu, HY; Fleming, TJ; Kamal, E; Wahlster, L; Pellin, D; Shimamura, A; Williams, DA; Sankaran, VG. Regulated GATA1 expression as a universal gene therapy for Diamond-Blackfan anemia. Cell Stem Cell. 2025; 32:38-52.e6.

Walder, TA; Odegard, EA; Meeds, HL; Kleiboeker, SB; Ziady, A; Sabulski, A; Jodele, S; Seif, AE; Davies, SM; Laskin, BL; Blackard, JT. Single-nucleotide polymorphisms within the BK polyomavirus non-coding control region are genotype-associated. Editor, Kwun HJ. Microbiology Spectrum. 2025; 13:e0049425.

Wang, C; Potts, DE; Sun, B; Toth, M; Ujhazi, B; Sharapova, S; Miller, R; Rosen, L; Yilmaz, M; Larsen, K; Strauss, KA; Holland, SM; Notarangelo, LD; Walter, JE. Factors associated with and kinetics of anti-IFN-α autoantibodies in RAG1/2 deficiency. Journal of Allergy and Clinical Immunology: Global. 2025; 4:100521.

Webster, A; Jodele, S; Luebbering, N; Davies, SM; Sabulski, DA. Single Cell Rnaseq Identifies Novel Graft Rejection Mechanisms and Resurgence of Recipient NK and T-Cells. Transplantation and Cellular Therapy. 2025; 31:s307-s308.

Wegehaupt, O; Borisov, O; Sieni, E; Oyen, F; Mann, J; Coniglio, ML; Chinnici, A; Pegoraro, F; Beneforti, L; Gilmour, K; Ghosh, S; Köttgen, A; Lehmberg, K; Ehl, S. Beyond genotype: challenges in predicting disease risk for carriers of biallelic perforin variants. Blood. 2025; 145:2992-3006.

Wendroth, R; Paisley, A; Marsh, R; Schulert, G; Wikenheiser-Brokamp, KA; Burg, G. Lung Disease in Systemic Juvenile Idiopathic Arthritis: An Atypical Path to Diagnosis. American Journal of Respiratory and Critical Care Medicine. 2025; 211:a7865.