Bone Marrow Transplantation and Immune Deficiency

Publications

Abdullah, S; Leever, G; Langenberg, L; Luebbering, N; Roskin, K; Webster, A; Jodele, S; Davies, SM; Sabulski, DA. Intra- and Inter-Organ Endothelial Cell Differences Contribute to TA-TMA through HMOX1, Hypoxia and Reactive Oxygen Species Signaling. Transplantation and Cellular Therapy. 2024; 30:s142.

Abraham, RS; Basu, A; Heimall, JR; Dunn, E; Yip, A; Kapadia, M; Kapoor, N; Satter, LF; Buckley, R; O'Reilly, R; Cowan, MJ; Puck, J; Dvorak, CC; Haddad, E. Relevance of lymphocyte proliferation to PHA in severe combined immunodeficiency (SCID) and T cell lymphopenia. Clinical Immunology. 2024; 261:109942.

Abts, MF; Silva-Carmona, M; Allen, JL; Doherty, EE; Baker, S; MacMillan, ML; Genatassio, A; Lacher, P; Griffin, T; Tekman, M; Edwards, SL; Woods, JC; Davies, SM; Goldfarb, SB. Success and Feasibility of Multiple Breath Washout: Prospective, Multi-Center Results from the Transpire Study. Transplantation and Cellular Therapy. 2024; 30:s142-s143.

Amarin, JZ; Dulek, DE; Simmons, J; Hayek, H; Chappell, JD; Nochowicz, CH; Kitko, CL; Schuster, JE; Muñoz, FM; Bocchini, CE; Englund, JA; Halasa, NB; Spieker, AJ; Kalams, SA. Immunophenotypic predictors of influenza vaccine immunogenicity in pediatric hematopoietic cell transplant recipients. Blood Advances. 2024; 8:1880-1892.

Auld, SC; Sheshadri, A; Alexander-Brett, J; Aschner, Y; Barczak, AK; Basil, MC; Cohen, KA; Cruz, CD; McGroder, C; Restrepo, MI; Staitieh, BS; Stek, C; Sun, J; Evans, SE. Postinfectious Pulmonary Complications: Establishing Research Priorities to Advance the Field: An Official American Thoracic Society Workshop Report. Annals of the American Thoracic Society. 2024; 21:1219-1237.

Aygun, B; Lane, A; Smart, LR; Santos, B; Tshilolo, L; Williams, TN; Olupot-Olupot, P; Stuber, SE; Tomlinson, G; Latham, T; Ware, RE. Hydroxyurea dose optimisation for children with sickle cell anaemia in sub-Saharan Africa (REACH): extended follow-up of a multicentre, open-label, phase 1/2 trial. The Lancet Haematology. 2024; 11:e425-e435.

Bartlett, AL; Wagner, JE; Jones, B; Wells, S; Sabulski, A; Fuller, C; Davies, SM. Fanconi anemia neuroinflammatory syndrome: brain lesions and neurologic injury in Fanconi anemia. Blood Advances. 2024; 8:3027-3037.

Bender, JD; Pillay-Smiley, N; Hill, GD; de Blank, P; Hummel, TR; Weiss, BD; Kumar, A; Zang, H; Ollberding, NJ; Ryan, TD. Cardiac Dysfunction in Children and Young Adults Treated With MEK Inhibitors: A Retrospective, Single-Center Study. JACC: CardioOncology. 2024; 6:794-796.

Bhatt, NS; Meyer, CL; Mau, LW; Auletta, JJ; Baker, KS; Broglie, L; Carpenter, PA; Choi, SW; Dandoy, CE; Devine, S; Phelan, R. Return to school practices after hematopoietic cell transplantation: a survey of transplant centers in the United States. Bone Marrow Transplantation. 2024; 59:653-659.

Bielamowicz, K; Dimitrion, P; Abla, O; Bomken, S; Campbell, P; Collin, M; Degar, B; Diamond, EL; Eckstein, OS; El-Mallawany, N; Shaw, PH; Wistinghausen, B; Rodriguez-Galindo, C; Allen, CE. Langerhans cell histiocytosis: NACHO update on progress, chaos, and opportunity on the path to rational cures. Cancer. 2024; 130:2416-2439.

Böhm, S; Wustrau, K; Pachlopnik Schmid, J; Prader, S; Ahlmann, M; Yacobovich, J; Beier, R; Speckmann, C; Behnisch, W; Ifversen, M; Lindemans, C; Henter, JI; Lehmberg, K; Ehl, S. Survival in primary hemophagocytic lymphohistiocytosis, 2016 to 2021: etoposide is better than its reputation. Blood. 2024; 143:872-881.

Carreras, E; Diaz-Ricart, M; Jodele, S; Penack, O; Vasu, S. Early Complications of Endothelial Origin. The EBMT Handbook. : Springer Nature; Springer Nature; 2024.

Chawla, EM; Schuler, CL; Barnhardt, EW; Herbst, LA; Sarkissian, A; McNeal-Trice, K; Newmeyer, A; Perry, M; Poynter, SE; Lannon, C. Integrating education for clinical practice change. The Clinical Teacher. 2024; 21:e13753.

Chi, SN; Lazow, M; Salloum, R; Lane, A; Hargrave, D; Witt, O; de Blank, P; Leary, SE S; Gorsi, H; Pierson, C; Yang, E; Mikael, L; Jones, DT W; Fouladi, M. TRLS-09. CONNECT1903: A PILOT AND SURGICAL STUDY OF LAROTRECTINIB FOR TREATMENT OF CHILDREN WITH NEWLY DIAGNOSED HGG WITH NTRK FUSION (NCT04655404). Neuro-Oncology. 2024; 26:0.

Chiang, S; Murguia-Favela, L; Wright, N; Steele, M; Seroogy, C; Blanchard-Rohner, G; Shrikhande, A; Wilson, J; Yang, L; Owsley, E; Derfalvi, B; Brager, R; Jordan, M; Marwaha, A. 68 LRBA dysfunction: a new diagnostic entity caused by biallelic LRBA missense variants results in reduced CTLA-4 expression and autoimmunity. Clinical Immunology. 2024; 262:110010.

Chiang, SC C; Covill, LE; Tesi, B; Campbell, TM; Schlums, H; Nejati-Zendegani, J; Mördrup, K; Wood, S; Theorell, J; Sekine, T; Horne, AC; Henter, JI; Meeths, M; Bryceson, YT. Efficacy of T-cell assays for the diagnosis of primary defects in cytotoxic lymphocyte exocytosis. Blood. 2024; 144:873-887.

Chokshi, SM; Odegard, EA; Meeds, HL; Kleiboeker, SB; Ziady, A; Sabulski, A; Jodele, S; Seif, AE; Davies, SM; Laskin, BL; Blackard, JT. Uncommon BK polyomaviruses detected in allogeneic hematopoietic cell transplant recipients. Microbiology Resource Announcements. 2024; 13.

Chokshi, SM; Odegard, EA; Meeds, HL; Kleiboeker, SB; Ziady, A; Sabulski, A; Jodele, S; Seif, AE; Davies, SM; Laskin, BL; Blackard, JT. Uncommon BK polyomaviruses detected in allogeneic hematopoietic cell transplant recipients. Editor, Matthijnssens J. Microbiology Resource Announcements. 2024; 13:e0000524.

Clark, D; Abdullah, S; Sabulski, DA; Towe, C; Langenberg, L; Davies, SM; Koo, DJ; Myers, KC. An in Vitro Patient-Derived Model of Bronchiolitis Obliterans Syndrome Yields New Insight into Steroid Sensitivity and Resistance. Transplantation and Cellular Therapy. 2024; 30:s252.

Cook, E; Dong, M; Chiang, SC C; Luedeke, D; Lake, KE; Hoerth, C; Deavy, M; Setchell, KD R; Zhao, J; Punt, N; Davies, SM; Marsh, RA; Mehta, P; Khandelwal, P. Ruxolitinib Pharmacokinetics and Pharmacodynamics in Children with Acute and Chronic Graft-versus-Host Disease. Transplantation and Cellular Therapy. 2024; 30:528.e1-528.e12.

Cournoyer, E; Ferrell, J; Sharp, S; Ray, A; Jordan, M; Dandoy, C; Grimley, M; Roy, S; Lorsbach, R; Merrow, AC; Nelson, A; Bartlett, A; Picarsic, J; Kumar, A. Dabrafenib and trametinib in Langerhans cell histiocytosis and other histiocytic disorders. Haematologica: the hematology journal. 2024; 109:1137-1148.

Dandoy, CE; Adams, J; Artz, A; Bredeson, C; Dahi, PB; Dodd, T; Jaglowski, S; Lehmann, L; LeMaistre, CF; Mian, A; Sorror, M; Steinberg, A; Viswabandya, A; Howard, DS. In Pursuit of Optimal Outcomes: A Framework for Quality Standards in Immune Effector Cell Therapy. Transplantation and Cellular Therapy. 2024; 30:942-954.

Dashti, HS; Wang, YM; Knauert, MP. Feeding critically ill patients at the right time of day. Critical Care (UK). 2024; 28:206.

de Oliveira, MH S; Abosamak, MF; Henry, BM; Benoit, SW; Lippi, G; Previdelli, I. Longitudinal serum chloride as a marker for poor prognosis in severely ill COVID-19 patients: A joint model approach. Brazilian Journal of Biometrics. 2024; 42:88-99.

Eissa, H; Thakar, MS; Shah, AJ; Logan, BR; Griffith, LM; Dong, H; Parrott, RE; O'Reilly, RJ; Dara, J; Kapoor, N; Haddad, E; Buckley, RH; Cowan, MJ; Heimall, J. Posttransplantation late complications increase over time for patients with SCID: A Primary Immune Deficiency Treatment Consortium (PIDTC) landmark study. Journal of Allergy and Clinical Immunology. 2024; 153:287-296.

Elgarten, CW; Grimley, M. Prophylactic VSTs: a promising start but still work to do. Blood Advances. 2024; 8:4738-4739.

Fidler, A; Chang, E; Dandoy, C; Beebe, D; Smith, D; Dye, T; Wang, YM. 0820 Challenges to Pediatric Patients Sleeping Well in the Hospital: Environmental and Practice Considerations. Sleep. 2024; 47:a351-a352.

Gorfinkel, L; Raghunandan, S; Watkins, B; Hebert, K; Neuberg, DS; Bratrude, B; Betz, K; Yu, A; Choi, SW; Davis, J; Horan, JT; Langston, A; Kean, LS; Qayed, M. Overlap chronic GVHD is associated with adverse survival outcomes compared to classic chronic GVHD. Bone Marrow Transplantation. 2024; 59:680-687.

Green, A; Rubinstein, JD; Grimley, M; Pfeiffer, T. Virus-Specific T Cells for the Treatment of Systemic Infections Following Allogeneic Hematopoietic Cell and Solid Organ Transplantation. Journal of the Pediatric Infectious Diseases Society. 2024; 13:S49-S57.

Grimley, M; Marón, GM; Gomez, CA; Prasad, VK; Dara, J; Lion, T; Papanicolaou, GA; Fukushima, K; Wynn, RF; Boeckh, MJ. Preliminary Results of a Phase 2a Clinical Trial to Evaluate Safety, Tolerability and Antiviral Activity of Intravenous Brincidofovir (BCV IV) in Immunocompromised Patients with Adenovirus Infection. Transplantation and Cellular Therapy. 2024; 30:s89.

Grom, AA; Canna, SW; Abu-Arja, RF; Sinha, R; Peixoto, L; Cannizzaro, E; Chandrakasan, S; Driest, K; Marsh, R; Neven, B; Schulert, G; Silva, JM F; Wall, D; Zeilhofer, U. Part 5: Allogeneic HSCT in refractory SJIA with lung disease; recent cases from centers in North America & Europe. Pediatric Rheumatology Online Journal. 2024; 21:86.

Grunebaum, E; Arnold, DE; Logan, B; Parikh, S; Marsh, RA; Griffith, LM; Mallhi, K; Chellapandian, D; Lim, SS; Deal, CL; Torgerson, TR; Malech, HL; Kang, EM; Leiding, JW. Allogeneic hematopoietic cell transplantation is effective for p47phox chronic granulomatous disease: A  Primary Immune Deficiency Treatment Consortium study. Journal of Allergy and Clinical Immunology. 2024; 153:1423-1431.e2.

Hambrick, HR; Fei, L; Pavia, K; Kaplan, J; Mizuno, T; Tang, P; Schuler, E; Benoit, S; Girdwood, ST. Cystatin C Outperforms Creatinine in Predicting Cefepime Clearance in Pediatric Stem Cell Transplant Recipients. Transplantation and Cellular Therapy. 2024; 30:614.e1-614.e11.

Hambrick, HR; Pavia, K; Tang Girdwood, S; Lazear, D; Taylor, JM; Benoit, S. Cefepime-Associated Neurotoxicity in a Pediatric Patient With Stage V Chronic Kidney Disease. Journal of Pharmacy Practice. 2024; 37:243-247.

Harms, FL; Rexach, JE; Efthymiou, S; Aynekin, B; Per, H; Güleç, A; Nampoothiri, S; Sampaio, H; Sachdev, R; Stoeva, R; Chard, M; Klassen, M; Pries, M; Kutsche, K. Loss of TBC1D2B causes a progressive neurological disorder with gingival overgrowth. European Journal of Human Genetics. 2024; 32:558-566.

Hasson, DC; Mohan, S; Rose, JE; Merrill, KA; Goldstein, SL; Benoit, SW; Varnell, CD. Ionized Magnesium Correlates With Total Blood Magnesium in Pediatric Patients Following Kidney Transplant. Annals of Laboratory Medicine. 2024; 44:21-28.

Henter, JI; Sieni, E; Eriksson, J; Bergsten, E; Hed Myrberg, I; Canna, SW; Coniglio, ML; Cron, RQ; Kernan, KF; Kumar, AR; Bottai, M; Bryceson, YT; Horne, AC; Jordan, MB. Diagnostic guidelines for familial hemophagocytic lymphohistiocytosis revisited. Blood. 2024; 144:2308-2318.

Huber, J; Dexheimer, J; Vaughn, L; Wall, J; O'Connor, G; Badia, P; Davies, SM; Dandoy, DC E. HSCT Patient and Family Education Concept Identification. Transplantation and Cellular Therapy. 2024; 30:s344-s345.

Hudda, Z; Flannery, A; Dilhoff, P; Webster, K; Jacobs, J; Strong, S; Detzel, J; Davies, SM; Khandelwal, P. Chronic Graft Versus Host Disease Adversely Affects School Performance and Quality of Life in Children and Young Adults. Transplantation and Cellular Therapy. 2024; 30:s43-s44.

Hudda, Z; Flannery, A; Teusink-Cross, A; Davies, SM; Khandelwal, P. Topical ruxolitinib is promising as sole or adjunctive therapy in treating maculopapular rash of acute and chronic skin GVHD. Bone Marrow Transplantation. 2024; 59:425-427.

Jodele, S; Dandoy, CE; Aguayo-Hiraldo, P; Lane, A; Teusink-Cross, A; Sabulski, A; Mizuno, K; Laskin, BL; Freedman, J; Davies, SM. A prospective multi-institutional study of eculizumab to treat high-risk stem cell transplantation-associated TMA. Blood. 2024; 143:1112-1123.

Kahn, J; Brazauskas, R; Bo-Subait, S; Buchbinder, D; Hamilton, BK; Schoemans, H; Abraham, AA; Agrawal, V; Auletta, JJ; Badawy, SM; Williams, KM; Vrooman, LM; Satwani, P; Phelan, R. Late effects after allogeneic haematopoietic cell transplantation in children and adolescents with non-malignant disorders: a retrospective cohort study. The Lancet Child and Adolescent Health. 2024; 8:740-750.

Khandelwal, P; Langenberg, L; Luebbering, N; Lake, KE; Butcher, A; Bota, K; Ramos, KN; Taggart, C; Choe, H; Vasu, S; Watanabe-Chailland, M; Haslam, DB; Lane, A; Davies, SM. A randomized phase 2 trial of oral vitamin A for graft-versus-host disease in children and young adults. Blood. 2024; 143:1181-1192.

Khandelwal, P; Pommert, L. Vitamin A to Keep GVHD Away: Single Oral High-Dose Vitamin A Before Bone Marrow Transplant Reduces Graft-Versus-Host Disease in Pediatric and Young Adult Patients. 2024; 21.

Khoury, R; Grimley, MS; Nelson, AS; Leemhuis, T; Cancelas, JA; Cook, E; Wang, YZ; Heyenbruch, D; Bollard, CM; Keller, MD; Hanley, PJ; Lutzko, C; Pham, G; Davies, SM; Rubinstein, JD. Third-party virus-specific T cells for the treatment of double-stranded DNA viral reactivation and posttransplant lymphoproliferative disease after solid organ transplant. American Journal of Transplantation. 2024; 24:1634-1643.

Klages, KL; Schwartz, LE; Crabtree, EJ S; Brokamp, C; Rasnick, E; Dandoy, CE; Davies, SM; Pai, AL H. Social determinants of health predict health outcomes following pediatric allogeneic hematopoietic stem cell transplant. Pediatric Blood and Cancer. 2024; 71:e30892.

Kögl, T; Chang, HF; Staniek, J; Chiang, SC C; Thoulass, G; Lao, J; Weißert, K; Dettmer-Monaco, V; Geiger, K; Manna, PT; Bryceson, YT; Ehl, S; Aichele, P; Ammann, S. Patients and mice with deficiency in the SNARE protein SYNTAXIN-11 have a secondary B cell defect. The Journal of Experimental Medicine. 2024; 221:e20221122.

Koo, DJ; Hornung, L; Sabulski, DA; Mehta, PA; Howell, JC; Davies, SM; Myers, KC. Longitudinal Bone Health in Patients with Fanconi Anemia and Other Major Inherited Bone Marrow Failure Syndromes. Transplantation and Cellular Therapy. 2024; 30:s291.

Koo, DJ; Huber, J; Badia, P; Dunseath, C; O'Connor, G; Davies, SM; Dandoy, DC E. Invasive Fungal Infections Are Rare in Pediatric and Young Adult Autologous Hematopoietic Stem Cell Transplant Patients. Transplantation and Cellular Therapy. 2024; 30:s122.

Koo, J; Hord, J; Gilliam, C; Rae, ML; Staubach, K; Nowacki, K; Lyren, A; Coffey, M; Dandoy, CE. Levofloxacin prophylaxis in pediatric oncology and hematopoietic stem cell transplantation: a literature review. Pediatric Hematology-Oncology (Informa). 2024; 41:432-448.

Koo, J; Howell, JC; Hornung, L; Sabulski, A; Mehta, PA; Davies, SM; Myers, KC. Infrequent fractures and resilient bone mineral density: bone health in patients with Fanconi anemia. Haematologica: the hematology journal. 2024; 109:3435-3438.

Koo, J; Huber, J; Badia, P; Dunseath, C; O'Connor, G; Davies, SM; Dandoy, CE. Invasive fungal infections are rare in pediatric and young adult autologous hematopoietic stem cell transplant patients. Pediatric Blood and Cancer. 2024; 71:e31336.

Koo, J; Langenberg, L; Luebbering, N; Strecker, L; Abdullah, S; Carusone, E; Deavy, M; Hoerth, C; Miller, G; Turner, D; Ziady, AG; Myers, KC; Jodele, S; Davies, SM. Ceramides Are Elevated in Transplant-Associated Thrombotic Microangiopathy in Hematopoietic Stem Cell Transplant Recipients and Are a Druggable Target for Prophylaxis. Transplantation and Cellular Therapy. 2024; 30:s17-s18.

Langenberg, L; Davies, SM; Koo, DJ. Hypusine Modulation in Hematopoietic Stem Cell Transplant Recipients: A Novel Insight into GI Gvhd Mechanisms. Transplantation and Cellular Therapy. 2024; 30:s250.

LeBlanc, FR; Grier, DD; Myers, KC; Shimamura, A; Pommert, L. A case of co-occurring acute myeloid leukemia and relapsed diffuse large B-cell lymphoma in a young adult with Shwachman-Diamond syndrome. Pediatric Blood and Cancer. 2024; 71:e31137.

Lee, BJ; Arter, Z; Doh, J; Griffin, SP; Vittayawacharin, P; Atallah, S; Shieh, KR; Tran, M; Jodele, S; Kongtim, P; Ciurea, SO. Eculizumab for Shiga-toxin-induced hemolytic uremic syndrome in adults with neurological involvement. ejHaem. 2024; 5:548-553.

Leever, G; Segev, N; Hornung, L; Myers, KC; Davies, SM; Howell, JC; Langenberg, L; Luebbering, N; Sabulski, DA. A Standardized Approach to Bone Health Screening in Pediatric HSCT and the Study of Bone Health Biomarkers. Transplantation and Cellular Therapy. 2024; 30:s348-s349.

Leon, MD; Otto, WR; Danziger-Isakov, L; Kumar, A; Huang, FS. Infectious Diseases Evaluation of the Child With Suspected Hemophagocytic Lymphohistiocytosis. Journal of the Pediatric Infectious Diseases Society. 2024; 13:220-227.

Luebbering, N; Abdullah, S; Roskin, K; Webster, A; Blackard, JT; Odegard, E; Laskin, B; Seif, AE; Jodele, S; Davies, SM; Sabulski, DA. Single Cell Rnaseq Identifies Chemokine Responses to BK Polyomavirus Infection and Novel Contribution of MAIT Cells. Transplantation and Cellular Therapy. 2024; 30:s84.

Marsh, RA. Salvage Therapy and Allogeneic Hematopoietic Cell Transplantation for the Severe Cytokine Storm Syndrome of Hemophagocytic Lymphohistiocytosis. Advances in Experimental Medicine and Biology. 2024; 1448:611-622.

McDonnell, J; Cousins, K; Younger, ME M; Lane, A; Abolhassani, H; Abraham, RS; Al-Tamemi, S; Aldave-Becerra, JC; Al-Faris, EH; Alfaro-Murillo, A; Lim, XR; Lopes, JP; López, AL; Tarquini, L. COVID-19 Vaccination in Patients with Inborn Errors of Immunity Reduces Hospitalization and Critical Care Needs Related to COVID-19: a USIDNET Report. Journal of Clinical Immunology. 2024; 44:86.

Meyer, AP; Barnett, CL; Myers, K; Siskind, CE; Moscarello, T; Logan, R; Roggenbuck, J; Rich, KA. Neuromuscular and cardiovascular phenotypes in paediatric titinopathies: a multisite retrospective study. Journal of medical genetics. 2024; 61:356-362.

Miranda, MA; Tsalatsanis, A; Trotter, JR; Arnold, DE; Squire, JD; Kidd, S; Parikh, S; Marsh, RA; Griffith, LM; Mallhi, K; Malech, HL; Kang, EM; Morton, FB; Leiding, JW. High symptom burden in female X-linked chronic granulomatous disease carriers. Clinical Immunology. 2024; 268:110364.

Morrison, A; Myers, K; Streich-Tilles, T. 5. Human Papillomavirus Vaccination Uptake in Adolescent Survivors of Bone Marrow Transplant. Journal of Pediatric and Adolescent Gynecology. 2024; 37:224.

Murphy, BN; Keenan-Pfeiffer, ME; Lane, A; Crosby, LE; Walsh, KE. Feasibility of a clinic-based, multicomponent hydroxyurea adherence intervention for adolescents and young adults with sickle cell disease. Pediatric Blood and Cancer. 2024; 71:e31144.

Pandurangi, S; Malik, A; Owens, J; Valencia, CA; Miethke, AG; Marsh, R; Chiang, S; Yang, L; Hopkin, R; Kasten, J; Huggins, J; Gutierrez Sanchez, LH; Castro-Rojas, C; Alquaraish, M. Deleterious variants in TNFAIP3 are associated with type II and seronegative pediatric autoimmune hepatitis. Journal of Hepatology. 2024; 80:e26-e28.

Papanicolaou, GA; Chen, M; He, N; Martens, MJ; Kim, S; Batista, MV; Bhatt, NS; Hematti, P; Hill, JA; Liu, H; Perales, MA; Chemaly, RF; Riches, M; Ustun, C. Incidence and Impact of Fungal Infections in Post-Transplantation Cyclophosphamide-Based Graft-versus-Host Disease Prophylaxis and Haploidentical Hematopoietic Cell Transplantation: A Center for International Blood and Marrow Transplant Research Analysis. Transplantation and Cellular Therapy. 2024; 30:114.e1-114.e16.

Potter, A; Wikenheiser-Brokamp, K; Hildeman, D; Sharma, N; Gu, M; Patel, K; Qureshi, M; Khan, MM; Wallace, C; Ziady, A; Hayes, D. (601) Decoding T Cell Clonal Dynamics in Acute Lung Rejection. The Journal of Heart and Lung Transplantation. 2024; 43:s293.

Power-Hays, A; Tomlinson, GA; Tshilolo, L; Santos, B; Williams, TN; Olupot-Olupot, P; Smart, LR; Aygun, B; Lane, A; Stuber, SE; Latham, T; Ware, RE. Reducing transfusion utilization for children with sickle cell anemia in sub-Saharan Africa with hydroxyurea: Analysis from the phase I/II REACH trial. American Journal of Hematology. 2024; 99:625-632.

Ramos, KN; Lake, KE; Hoerth, C; Langenberg, L; Luebbering, N; Haslam, D; Newburg, D; Morrow, AL; Ollberding, NJ; Denson, LA; Watanabe-Chailland, M; Romick-Rosendale, L; Davies, SM; Khandelwal, P. Administration of Human Milk Oligosaccharide (2′-fucosyllactose) Reduces Dysbiosis and Increases Short Chain Fatty Acids in Children and Young Adults Following HSCT: A Prospective, Single-Center Study. Transplantation and Cellular Therapy. 2024; 30:s16.

Ramos, KN; Langenberg, L; Strecker, L; Luebbering, N; Davies, SM; Khandelwal, P. Lower Levels of the Vitamin A Transporter Serum Amyloid A1 (SAA1) Are Associated with Improved HSCT Outcomes in Children and Young Adults. Transplantation and Cellular Therapy. 2024; 30:s134-s135.

Ramos, KN; Leino, D; Luebbering, N; Grimley, M; Badia, P; Davies, SM; Khandelwal, P. Successful Use of Teduglutide As Adjunctive Therapy in the Management of GI GvHD in Children and Young Adults: A Single Center Case Series. Transplantation and Cellular Therapy. 2024; 30:s136.

Ramos, KN; Leino, D; Luebbering, N; Grimley, MS; Badia, P; Davies, SM; Khandelwal, P. Use of Teduglutide in the Management of Gastrointestinal Graft-versus-Host Disease in Children and Young Adults. Transplantation and Cellular Therapy. 2024; 30:454.e1-454.e6.

Rayes, A; Logan, B; Liu, X; Dara, J; Buckley, RH; Oved, JH; Kapoor, N; Kapadia, M; Chandra, S; Martinez, C; Heimall, JR; Haddad, E; Pai, S; Dvorak, CC. Outcomes Following Matched Sibling Donor Transplant for Severe Combined Immunodeficiency: A Report from the Pidtc. Transplantation and Cellular Therapy. 2024; 30:s92-s93.

Rotz, SJ; Hamilton, BK; Wei, W; Ahmed, I; Winston, SA; Ballard, S; Bernard, RJ; Carpenter, P; Farhadfar, N; Ferraro, C; Tomlinson, K; Whiteside, S; Wiedl, C; Myers, K. Fertility Potential and Gonadal Function in Survivors of Reduced-Intensity Hematopoietic Stem Cell Transplantation. Transplantation and Cellular Therapy. 2024; 30:534.e1-534.e13.

Rumlow, Z; Almodallal, Y; Zimmerman, MB; Miner, R; Asbury, R; Knake, LA; Schmitz, A. The Impact of Diagnosis-Specific Plan Templates on Admission Note Writing Time: A Quality Improvement Initiative. Journal of Graduate Medical Education. 2024; 16:581-587.

Sabulski, A; Pommert, L. Eculizumab: Inhibiting C5 Earns a High Five in Prospective Pediatric, Multicenter, High-risk Transplant-associated Thrombotic Microangiopathy Study. 2024; 21.

Sabulski, DA; Langenberg, L; Luebbering, N; Libermann, TA; Dillon, ST; Koo, J; Myers, KC; Jodele, S; Davies, SM. Plasma Proteome Analyses Identify Predictors of Graft Rejection Prior to Stem Cell Infusion and Support Interferon-Mediated Ferroptosis As a Novel Mechanism of Graft Rejection. Transplantation and Cellular Therapy. 2024; 30:s4-s5.

Sarkar, N; Myers, KC; Lane, A; Davies, SM; Benoit, SW. Pre-transplant glomerular hyperfiltration is not a risk factor for increased renal morbidity and mortality in pediatric stem cell transplant patients. Pediatric Blood and Cancer. 2024; 71:e30853.

Satty, AM; Klein, E; Mauguen, A; Kunvarjee, B; Boelens, JJ; Cancio, M; Curran, KJ; Kernan, NA; Prockop, SE; Scaradavou, A; Torok-Castanza, J; Mehta, PA; O’Reilly, RJ; Boulad, F. T-cell depleted allogeneic hematopoietic stem cell transplant for the treatment of Fanconi anemia and MDS/AML. Bone Marrow Transplantation. 2024; 59:23-33.

Schoettler, ML; Lehmann, L; Kao, PC; Chen, N; Jodele, S; Chonat, S; Williams, KM; London, WB; Duncan, C; Dandoy, C. Pediatric transplant-associated thrombotic microangiopathy health care utilization and implications of eculizumab therapy. Blood Advances. 2024; 8:1220-1233.

Schuster, JE; Hamdan, L; Dulek, DE; Kitko, CL; Batarseh, E; Haddadin, Z; Stewart, LS; Stahl, A; Potter, M; Rahman, H; Munoz, FM; Danziger-Isakov, L; Spieker, AJ; Halasa, NB. The Durability of Antibody Responses of Two Doses of High-Dose Relative to Two Doses of Standard-Dose Inactivated Influenza Vaccine in Pediatric Hematopoietic Cell Transplant Recipients: A Multi-Center Randomized Controlled Trial. Clinical Infectious Diseases. 2024; 78:217-226.

Shanthikumar, S; Goldfarb, S; Abts, M; Barochia, A; Bergeron, A; Blinman, T; Bracken, J; Calvo, C; Casey, A; Charbek, E; Teusink-Cross, A; Towe, CT; Walkup, LL; Yanik, GA. Detection of Bronchiolitis Obliterans Syndrome after Pediatric Hematopoietic Stem Cell Transplantation: An Official American Thoracic Society Clinical Practice Guideline. American Journal of Respiratory and Critical Care Medicine. 2024; 210:262-280.

Shanthikumar, S; Gower, WA; Cooke, KR; Bergeron, A; Schultz, KR; Barochia, A; Tamae-Kakazu, M; Charbek, E; Reardon, EE; Calvo, C; Towe, CT; Yanik, GA; Iyer, NP; Goldfarb, SB. Diagnosis of Post-Hematopoietic Stem Cell Transplantation Bronchiolitis Obliterans Syndrome in Children: Time for a Rethink?. Transplantation and Cellular Therapy. 2024; 30:760-769.

Shimamura, A; Myers, K; Andresen, F; Zhou, Y; Reed, H; Do, H; Weller, E. 1002 – BONE MARROW FAILURE AND CLONAL EVOLUTION. Experimental Hematology. 2024; 137:104303.

Shimano, KA; Rothman, JA; Allen, SW; Castillo, P; de Jong, JL O; Dror, Y; Geddis, AE; Lau, BW; McGuinn, C; Narla, A; Myers, K; Gloude, NJ; Broglie, L; Boklan, J. Treatment of newly diagnosed severe aplastic anemia in children: Evidence-based recommendations. Pediatric Blood and Cancer. 2024; 71:e31070.

Shimano, KA; Sasa, G; Broglie, L; Gloude, NJ; Myers, K; Nakano, TA; Sharathkumar, A; Rothman, JA; Pereda, MA; Overholt, K; de Jong, JL O; Castillo, P; Allen, SW; Boklan, J. Treatment of relapsed/refractory severe aplastic anemia in children: Evidence-based recommendations. Pediatric Blood and Cancer. 2024; 71:e31075.

Siefert, M; Rheiner, S; Ziady, A; Lin, S. 269 Modulating nucleolin trafficking can significantly enhance DNA nanoparticle-mediated gene expression in the lung. Journal of Cystic Fibrosis. 2024; 23:s143.

Siefert, ME; Skala, EJ; Potter, AS; Hayes, D; Ziady, A. (1358) Plasma and Bronchoalveolar Fluid Proteomes Identify Similar Pathways Associated with Allograft Dysfunction in Individual LTx Recipients with Different Underlying Conditions. The Journal of Heart and Lung Transplantation. 2024; 43:s625-s626.

Siegert, TF; Opoka, RO; Nakafeero, M; Carman, A; Mellencamp, KA; Latham, T; Hume, H; Lane, A; Ware, RE; Ssenkusu, JM; John, CC; Conroy, AL. Angiopoietin-2 is associated with sickle cell complications, including stroke risk, and decreases with hydroxyurea therapy. 2024; 1:100001.

Skala, E; Banerjee, R; Siefert, M; Dusa, C; Stevens, C; Hils, B; Bdaiwi, A; Hayes, D; Cleveland, Z; Ziady, A. 846 Plasma proteomics identifies changes in disease-associated pathways in subjects with CF bronchiectasis after elexacaftor/tezacaftor/ivacaftor initiation. Journal of Cystic Fibrosis. 2024; 23:s490.

Skala, EJ; Siefert, ME; Potter, AS; Sharma, N; Hayes, D; Ziady, AG. (610) Bronchoalveolar Lavage and Plasma Proteomes Identify Features of Disease That Segregate Lung Transplant Recipients with versus without Bronchiolitis Obliterans Syndrome. The Journal of Heart and Lung Transplantation. 2024; 43:s297.

Snyder, AJ; Campbell, KM; Lane, A; Mehta, PA; Myers, K; Davies, SM; Koo, J. Liver abnormalities are frequent and persistent in patients with Fanconi anemia. Blood Advances. 2024; 8:1427-1438.

Snyder, AJ; Miller, E; O'Conner, A; Campbell, KM; Mehta, PA; Myers, KC; Davies, SM; Koo, DJ. Frequent Fanconi Anemia-Associated Liver Abnormalities before and after HSCT. Transplantation and Cellular Therapy. 2024; 30:s291-s292.

Spears, K; Goodin, CS; Meyer, R; Kusnier, K; Haslam, D; Dandoy, DC E; Davies, SM; Badia, P. The Scrubbing Olympics. Transplantation and Cellular Therapy. 2024; 30:s69-s70.

Strecker, L; Towe, C; Sabulski, DA; Langenberg, L; Libermann, TA; Dillon, ST; Gu, X; Davies, SM; Koo, DJ; Myers, KC. Proteomic Analysis of Bronchoalveolar Lavage Fluid from Children with Bronchiolitis Obliterans Syndrome Identifies Potential Treatment Strategies. Transplantation and Cellular Therapy. 2024; 30:s252-s253.

Takahashi, T; Lake, AJ; Wachter, F; Calderon, FA; Dandoy, C; Keating, AK. Effects of Total Body Irradiation on Hematopoietic Cell Transplantation Outcomes in Pediatric Acute Myeloid Leukemia with Prior Central Nervous System Involvement. Transplantation and Cellular Therapy. 2024; 30:812.e1-812.e11.

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Uschner, D; Sverdlov, O; Carter, K; Chipman, J; Kuznetsova, O; Renteria, J; Lane, A; Barker, C; Geller, N; Proschan, M; Posch, M; Tarima, S; Bretz, F; Rosenberger, WF. Using Randomization Tests to Address Disruptions in Clinical Trials: A Report from the NISS Ingram Olkin Forum Series on Unplanned Clinical Trial Disruptions. Statistics in Biopharmaceutical Research. 2024; 16:405-413.

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Vasu, S; Bejanyan, N; Miller, EG; Elder, P; Zhao, Q; Davies, SM; Hahn, TE. TA-TMA Is Frequent, but Not All TA-TMA Is Actionable in Adult Allogeneic HCT Patients: A Report from the MIDAS (Microangiopathy, Endothelial Damage in Adults undergoing Stem cell transplantation) Consortium. Transplantation and Cellular Therapy. 2024; 30:s19.

Verkamp, B; Jodele, S; Marsh, RA; Sabulski, DA; Davies, SM; Jordan, MB. Emapalumab Therapy Prior to Hematopoietic Stem Cell Transplant Is Associated with Improved Long-Term Chimerism and Event-Free Survival in Pediatric Patients with Hemophagocytic Lymphohistiocytosis. Transplantation and Cellular Therapy. 2024; 30:s93.

Vicente-Muñoz, S; Davis, JC; Lane, A; Lane, AN; Waltz, SE; Wells, SI. Lipid profiling of RON and DEK-dependent signaling in breast cancer guides discovery of gene networks predictive of poor outcomes. Frontiers in Oncology. 2024; 14:1382986.

Walder, TA; Odegard, EA; Meeds, HL; Kleiboeker, SB; Ziady, A; Sabulski, A; Jodele, S; Seif, AE; Davies, SM; Laskin, BL; Blackard, JT. Rare BK polyomavirus subtype III detected in hematopoietic cell transplant recipient. Editor, Matthijnssens J. Microbiology Resource Announcements. 2024; 13:e0067624.

Wang, C; Sun, B; Wu, K; Farmer, JR; Ujhazi, B; Geier, CB; Gordon, S; Westermann-Clark, E; Savic, S; Secord, E; Wang, W; Wang, JY; Wang, X; Walter, JE. Clinical, immunological features, treatments, and outcomes of autoimmune hemolytic anemia in patients with RAG deficiency. Blood Advances. 2024; 8:603-607.

Wang, YZ M; Huber, JF; Flesch, L; Demmel, K; Lane, A; Beebe, DW; Crosby, LE; Hogenesch, JB; Smith, DF; Davies, SM; Dandoy, CE. Trajectory of Sleep, Depression, and Quality of Life in Pediatric HSCT Recipients. Transplantation and Cellular Therapy. 2024; 30:632.e1-632.e5.

Wang, YZ M; Kaj-Carbaidwala, B; Lane, A; Agarwal, S; Beier, F; Bertuch, A; Borovsky, KA; Brennan, SK; Calado, RT; Catto, LF B; Simonetto, DA; Ziegler, DS; Miethke, AG; Myers, KC. Liver disease and transplantation in telomere biology disorders: An international multicenter cohort. Hepatology Communications. 2024; 8:e0462.

Xu, J; Fei, P; Simon, DW; Morowitz, MJ; Mehta, PA; Du, W. Crosstalk between DNA Damage Repair and Metabolic Regulation in Hematopoietic Stem Cells. Cells. 2024; 13:733.

Xu, X; Denton, J; Wu, Y; Liu, J; Guan, Q; Dawson, DB; Bleesing, J; Zhang, W. Genetic Testing in Patients with Autoimmune Lymphoproliferative Syndrome: Experience of 802 Patients at Cincinnati Children's Hospital Medical Center. Journal of Clinical Immunology. 2024; 44:166.

Zinter, MS; Brazauskas, R; Strom, J; Chen, S; Bo-Subait, S; Sharma, A; Beitinjaneh, A; Dimitrova, D; Guilcher, G; Preussler, J; Winestone, L; Duncan, C; Phelan, R; Dvorak, CC. Intensive care risk and long-term outcomes in pediatric allogeneic hematopoietic cell transplant recipients. Blood Advances. 2024; 8:1002-1017.